| Suspended | Methadone as an Alternative Treatment for Children Underdoing HSCT NCT06940570 | University of Texas Southwestern Medical Center | Phase 3 |
| Not Yet Recruiting | CK0801 for Treatment of Aplastic Anemia NCT07499102 | Cellenkos, Inc. | Phase 2 |
| Not Yet Recruiting | UI-Romi-02; Romiplostim Added to Standard of Care for Treatment Naive and Relapsed or Refractory Severe Aplast NCT07001254 | Anjali Sharathkumar | Phase 2 |
| Not Yet Recruiting | Romiplostim N01 in the Treatment of Refractory Chemoradiotherapy-induced AA NCT07532408 | Peking Union Medical College Hospital | Phase 2 |
| Not Yet Recruiting | The Safety and Efficacy of Daratumumab in Patients With Refractory Aplastic Anemia NCT07287228 | Institute of Hematology & Blood Diseases Hospital, China | Phase 1 / Phase 2 |
| Recruiting | A Prediction Model in Pregnant Women With Aplastic Anemia NCT07101770 | Peking University People's Hospital | — |
| Recruiting | Ruxolitinib Based GVHD Prophylaxis Regimen Before, During, and After Hematopoietic Cell Transplantation in Old NCT06752694 | Fred Hutchinson Cancer Center | Phase 2 |
| Recruiting | Reproductive and Mental Health of Patients With Aplastic Anemia NCT06936930 | Institute of Hematology & Blood Diseases Hospital, China | — |
| Not Yet Recruiting | Study of CM313(SC) Injection in Subjects With Relapsed/Refractory Aplastic Anemia NCT06791824 | Keymed Biosciences Co.Ltd | Phase 1 / Phase 2 |
| Recruiting | Let's Get REAL: Family Health Communication Tool in Pediatric Stem Cell Transplant and Cellular Therapy NCT06689800 | Washington University School of Medicine | N/A |
| Not Yet Recruiting | Effects of Levetiracetam Monotherapy on Various Hematological Parameters in Adult Patients Suffering of Epilep NCT06491303 | Assiut University | — |
| Not Yet Recruiting | Indication of HSCT in Patients With Refractory/Relapse AA After First-line Standard Immunosuppressive Therapy NCT06646497 | Assistance Publique - Hôpitaux de Paris | Phase 2 |
| Recruiting | Standard Immunosuppressive Therapy Combined With Romiplostim N01 as First-line Treatment for Severe Aplastic A NCT06613880 | Institute of Hematology & Blood Diseases Hospital, China | Phase 2 |
| Recruiting | CD7 CAR-T Bridging to alloHSCT for Severe Aplastic Anemia NCT06633328 | Zhejiang University | EARLY_Phase 1 |
| Recruiting | Darzalex Faspro (Daratumumab and Hyaluronidase-fihj) Before Standard Desensitization and Allogeneic Peripheral NCT06398457 | Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins | EARLY_Phase 1 |
| Not Yet Recruiting | A Study of Romiplostim for the Treatment of Refractory Transfusion-dependent NSAA NCT06535685 | Peking Union Medical College Hospital | Phase 4 |
| Not Yet Recruiting | Efficacy and Safety of rhTPO in Combination With Cyclosporine Versus Cyclosporine Alone in the Treatment of TD NCT06525948 | Peking Union Medical College Hospital | Phase 4 |
| Not Yet Recruiting | Ropustin for Refractory Aplastic Anaemia After Radiotherapy - a Single-centre, Prospective, Open-label, Single NCT06516484 | Peking Union Medical College Hospital | Phase 4 |
| Not Yet Recruiting | NAC for Hematopoietic Recovery in SAA NCT06518044 | Peking University People's Hospital | Phase 2 |
| Recruiting | Revolade Tablets Specified Drug-use Survey NCT06287268 | Novartis Pharmaceuticals | — |
| Not Yet Recruiting | A Prospective Study on the Treatment of Recurrent/Refractory/Intolerable NSAA With Lusutrombopag NCT06426043 | Peking Union Medical College Hospital | Phase 4 |
| Recruiting | A Study of Emapalumab for Pediatric Aplastic Anemia NCT06430788 | Memorial Sloan Kettering Cancer Center | Phase 2 |
| Not Yet Recruiting | Luspatercept Plus CsA vs CsA for the Treatment of Newly Diagnosed Non-Transfusion-Dependent NSAA NCT06424639 | Peking Union Medical College Hospital | Phase 4 |
| Active Not Recruiting | ATGAM General Investigation NCT06039020 | Pfizer | — |
| Completed | CsA+ATG+AVA vs. CsA+AVA for the Treatment of Newly-diagnosed SAA in the Elderly NCT05996393 | Peking Union Medical College Hospital | Phase 4 |
| Recruiting | High-Altitude Hematology Observation-Stem Cell Transplantation (HALO-SCT) NCT07205523 | Yigeng Cao,MD,PhD | — |
| Unknown | Efficacy and Safety of CsA+AVA in the Treatment of NSAA in the Elderly NCT06004752 | Peking Union Medical College Hospital | Phase 2 |
| Unknown | A Prospective, Randomized, Controlled Study of rhTPO in Combination With Herombopag + CsA vs Herombopag + CsA NCT06004791 | Peking Union Medical College Hospital | Phase 4 |
| Completed | A Study of the Safety and Effectiveness of Eltrombopag in Combination With Immunosuppressive Therapy (IST) in NCT07415083 | Novartis Pharmaceuticals | — |
| Completed | Efficacy of Daratumumab to Overcome Platelet Transfusion Refractoriness in Patients with Aplastic Anemia NCT05832216 | Institute of Hematology & Blood Diseases Hospital, China | Phase 1 |
| Recruiting | Exercise Training and NR Supplementation Trial to Improve Fitness in AYA HCT Survivors NCT05194397 | Children's Hospital of Philadelphia | Phase 2 |
| Unknown | Efficacy of IST Combined With TPO-RA in the Treatment of AA and Establishment of a Recurrence Prediction Syste NCT06009965 | Peking Union Medical College Hospital | Phase 4 |
| Completed | Efficacy and Safety in Transfusion Independent Non-severe Aplastic Anemia NCT05399732 | Bing Han | Phase 2 |
| Unknown | Autologous Tregs for Aplastic Anaemia NCT05386264 | King's College Hospital NHS Trust | Phase 1 |
| Unknown | Efficacy and Safety of Avatrombopag Combined With IST for the Treatment of HAAA and SAA With Abnormal Liver Fu NCT05571332 | Institute of Hematology & Blood Diseases Hospital, China | N/A |
| Not Yet Recruiting | An Observational, Multicenter Study to Evaluate the Safety and Effectiveness of Hetrombopag in Patients With I NCT05333861 | Union Hospital, Tongji Medical College, Huazhong University of Science and Technology | — |
| Unknown | GVHD Prophylaxis by Addition of CD20 Monoclonal Antibody to the Conditioning Regimen in SAA With Treatment of NCT05510505 | The First Affiliated Hospital of Soochow University | Phase 2 |
| Recruiting | Two Step Haplo With Radiation Conditioning NCT05031897 | Thomas Jefferson University | Phase 2 |
| Unknown | Efficacy and Safety of Hetrombopag in Non-severe Aplastic Anemia NCT05018936 | Peking Union Medical College Hospital | Phase 2 / Phase 3 |
| Completed | Geriatric Optimization Plan to Improve Survival in Older Adult Allogeneic Hematopoietic Cell Transplant Candid NCT05972577 | Ohio State University Comprehensive Cancer Center | N/A |
| Unknown | The Evaluating Multidisciplinary Bone Marrow Failure Care in Bone Marrow Failure and Related Disorders. NCT04819607 | Peter MacCallum Cancer Centre, Australia | — |
| Active Not Recruiting | Long Term Follow-up Observational Study After Clinical Trials of AMG531 (Romiplostim) in Patients With Untreat NCT04870346 | Kyowa Kirin Co., Ltd. | — |
| Unknown | Quantitative MRI of Bone Marrow Fat Fraction in Patients With Trepanobiopsy NCT04761965 | Federal Research Institute of Pediatric Hematology, Oncology and Immunology | N/A |
| Unknown | Avatrombopag Usage in NSAA NCT04728789 | Peking Union Medical College Hospital | Phase 2 / Phase 3 |
| Recruiting | Haploidentical HCT for Severe Aplastic Anemia NCT04558736 | St. Jude Children's Research Hospital | Phase 2 |
| Recruiting | National Longitudinal Cohort of Hematological Diseases NCT04645199 | Institute of Hematology & Blood Diseases Hospital, China | — |
| Completed | Ibrutinib for the Treatment of COVID-19 in Patients Requiring Hospitalization NCT04439006 | Jennifer Woyach | Phase 1 |
| Completed | TPO-Mimetic Use in Children for Hematopoietic Failure NCT04478227 | Anjali Sharathkumar | EARLY_Phase 1 |
| Completed | A Study to Assess Efficacy and Safety of PF-06462700 in Japanese Participants With Aplastic Anemia NCT04350606 | Pfizer | Phase 3 |
| Completed | Efficacy and Safety of Eltrombopag + Tacrolimus in Chinese Refractory or Relapsed Aplastic Anemia Patients NCT04403321 | Peking Union Medical College Hospital | Phase 2 |
| Completed | Study Assessed the Safety and Efficacy of Eltrombopag in Chinese Refractory or Relapsed Severe Aplastic Anemia NCT03988608 | Novartis Pharmaceuticals | Phase 2 |
| Completed | Study of AMG531 (Romiplostim) in Patients With Aplastic Anemia NCT04095936 | Kyowa Kirin Co., Ltd. | Phase 2 / Phase 3 |
| Completed | Combination of Thrombopoietin Mimetic and Immunosuppressive Therapy in Aplastic Anaemia NCT03896971 | Safaa AA Khaled | Phase 4 |
| Completed | Electronic Patient-reported Outcome Monitoring in Aplastic Anemia and Paroxysmal Nocturnal Hemoglobinuria NCT04128943 | University Hospital, Basel, Switzerland | — |
| Unknown | Screening Gene Mutations in Myeloid Cancers by Next Generation Sequencing to Improve Treatment Results NCT04060485 | National Taiwan University Hospital | — |
| Active Not Recruiting | Cytokine-Treated Veto Cells in Treating Patients With Hematologic Malignancies Following Stem Cell Transplant NCT03622788 | M.D. Anderson Cancer Center | Phase 1 / Phase 2 |
| Completed | Study of AMG531(Romiplostim) in Patients With Aplastic Anemia NCT03957694 | Kyowa Kirin Co., Ltd. | Phase 2 / Phase 3 |
| Unknown | Risk Stratification Directed Conditioning Regimen for Haploidentical HSCT in SAA NCT03821987 | Peking University People's Hospital | N/A |
| Completed | Posaconazole Prophylaxis During ATG Treatment for hMDS/AA Patients NCT03318159 | Seoul National University Hospital | Phase 2 |
| Unknown | Total Body Irradiation Treatments for Patients Treated at European Institute of Oncology NCT06335277 | European Institute of Oncology | — |
| Unknown | Ambispective Observational Study to Evaluate the Incidence and Management of Aplastic Anemia in Spain NCT04001686 | Biogipuzkoa Health Research Institute | — |
| Unknown | Clinical Study of Non Severe Aplastic Anemia Treated With Cyclosporine, Androgen and Levamisole NCT03218657 | Shengyun Lin | N/A |
| Terminated | Fludarabine Phosphate, Cyclophosphamide, Total Body Irradiation, and Donor Stem Cell Transplant in Treating Pa NCT03333486 | Roswell Park Cancer Institute | Phase 2 |
| Unknown | Effects of Aerobic Training and Inspiratory Muscle Training in Patients During Hematopoietic Stem Cell Transpl NCT03373526 | Daniel Godoy Martinez | N/A |
| Completed | A Randomized Phase IV Control Trial of Single High Dose Oral Vitamin D3 in Pediatric Patients Undergoing HSCT NCT03176849 | Phoenix Children's Hospital | Phase 4 |
| Completed | A Phase II Dose-escalation Study Characterizing the PK of Eltrombopag in Pediatric Patients With Previously Un NCT03025698 | Novartis Pharmaceuticals | Phase 2 |
| Withdrawn | Patient-Driven Transfusion Thresholds in Hematological Disorders: A Pilot Study NCT03086252 | Emory University | N/A |
| Unknown | ATG Combined With Cyclophosphamide And Cord Blood Transfusion in Treating Patients With Severe Aplastic Anemia NCT02838992 | Jinan Military General Hospital | Phase 4 |
| Completed | Engineered Donor Stem Cell Transplant in Treating Patients With Hematologic Malignancies NCT02960646 | M.D. Anderson Cancer Center | Phase 1 |
| Unknown | Umbilical Cord Derived Mesenchymal Stem Cells Therapy in Aplastic Anemia NCT03055078 | Hebei Medical University | Phase 1 |
| Completed | King's Invasive Aspergillosis Study II NCT02875743 | King's College Hospital NHS Trust | Phase 4 |
| Unknown | Study of MRI Monitoring in Patients With Aplastic Anemia and Low or Int-1 Risk of MDS Complicated With Iron Ov NCT02833493 | Peking Union Medical College Hospital | — |
| Completed | NMA Haplo or MUD BMT for Newly Diagnosed Severe Aplastic Anemia NCT02833805 | Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins | Phase 2 |
| Completed | Study of Romiplostim(AMG531) in Subjects With Aplastic Anemia NCT02773290 | Kyowa Kirin Co., Ltd. | Phase 2 / Phase 3 |
| Completed | Reduced Intensity Chemotherapy and Radiation Therapy Before Donor Stem Cell Transplant in Treating Patients Wi NCT02566304 | Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University | Phase 2 |
| Completed | Phase IIA Open Label Study to Evaluate Efficacy and Safety of BL-8040 Followed by (hATG), Cyclosporine and Met NCT02462252 | BioLineRx, Ltd. | Phase 2 |
| Recruiting | Umbilical Cord Blood Transplantation From Unrelated Donors NCT03016806 | University of Rochester | — |
| Completed | Eltrombopag in Combination With Rabbit Anti-thymocyte Globulin/Cyclosporine A in Naive Aplastic Anemia (AA) Su NCT02404025 | Novartis Pharmaceuticals | Phase 2 |
| Completed | Hematopoietic Stem Cell Transplant for Dyskeratosis Congenita or Severe Aplastic Anemia NCT02162420 | Masonic Cancer Center, University of Minnesota | N/A |
| Completed | Fertility Preservation in Women Who Will Have Gonadotoxic Therapy or Hematopoetic Stem Cell Transplantation, a NCT02225145 | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | — |
| Completed | A Single-Arm Phase 2 Study With Optimized Standard Protocol for Severe Aplastic Anemia NCT02203396 | Institute of Hematology & Blood Diseases Hospital, China | Phase 2 |
| Terminated | Safety and Efficacy of Exjade in the Treatment of Transfusion-dependent Iron Overload in Aplastic Anemia Patie NCT01818726 | Novartis Pharmaceuticals | Phase 4 |
| Completed | A Phase 2 Study to Evaluate the Efficacy and Safety of AMG531 in Aplastic Anemia NCT02094417 | Kyowa Kirin Korea Co., Ltd. | Phase 2 |
| Completed | Nandrolone Decanoate in the Treatment of Telomeropathies NCT02055456 | University of Sao Paulo | Phase 1 / Phase 2 |
| Unknown | Open-label Clinical Trial to Investigate the Safety and Tolerability of Allogeneic B-cell Concentrates for Imm NCT02007811 | University of Erlangen-Nürnberg Medical School | Phase 1 / Phase 2 |
| Unknown | Comparison of Two Different Doses of Rabbit ATG-Fresenius With Cyclosporin in the Treatment of Acquired Aplast NCT02028416 | National Institute of Blood Disease Center, Pakistan | N/A |
| Completed | Identification of Mechanism in the Erythroid Response in Patients With Myelodysplasia Undergoing Chelation The NCT01956799 | Fondazione Italiana Sindromi Mielodisplastiche-ETS | — |
| Unknown | Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Subclinical Paroxysmal Nocturn NCT01760096 | Institute of Hematology & Blood Diseases Hospital, China | Phase 2 |
| Completed | Reduced-Intensity Conditioning Before Donor Stem Cell Transplant in With High-Risk Hematologic Malignancies NCT01760655 | Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University | Phase 2 |
| Completed | Bone Marrow and Kidney Transplant for Patients With Chronic Kidney Disease and Blood Disorders NCT01758042 | Massachusetts General Hospital | N/A |
| Active Not Recruiting | Radiation- and Alkylator-free Bone Marrow Transplantation Regimen for Patients With Dyskeratosis Congenita NCT01659606 | Boston Children's Hospital | Phase 2 |
| Unknown | Safety and Efficacy of Levamisole Combined With Cyclosporine A in Patients With Classic Paroxysmal Nocturnal H NCT01642979 | Institute of Hematology & Blood Diseases Hospital, China | Phase 2 |
| Recruiting | Methylprednisolone, Horse Anti-Thymocyte Globulin, Cyclosporine, Filgrastim, and/or Pegfilgrastim or Pegfilgra NCT01624805 | M.D. Anderson Cancer Center | Phase 2 |
| Unknown | Moderate-dose Cyclophosphamide for Childhood Acquired Aplastic Anemia NCT01995331 | Xiaofan Zhu | Phase 4 |
| Completed | Fludarabine Phosphate, Melphalan, and Low-Dose Total-Body Irradiation Followed by Donor Peripheral Blood Stem NCT01529827 | Roswell Park Cancer Institute | Phase 2 |
| Terminated | Pooled Unrelated Donor Umbilical Cord Blood Transplant For Hematologic Malignancy Needing Allogeneic Stem Cell NCT01500161 | Texas Oncology Cancer Center | Phase 2 |
| Completed | A Two-Step Approach to Reduced Intensity Bone Marrow Transplant for Patients With Hematological Malignancies NCT01384513 | Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University | Phase 2 |
| Completed | Danazol for Genetic Bone Marrow and Lung Disorders NCT01441037 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 1 / Phase 2 |
| Withdrawn | Alemtuzumab and Rituximab in Aplastic Anemia NCT01408342 | Hospital Universitario Dr. Jose E. Gonzalez | N/A |
| Terminated | Alefacept in Patients With Relapsed/Refractory Aplastic Anemia NCT01267643 | The Cleveland Clinic | Phase 1 |
| Terminated | Trial of Two Central Venous Catheter (CVC) Flushing Schemes in Pediatric Hematology and Oncology Patients NCT01343680 | Alberta Children's Hospital | Phase 3 |
| Completed | High-Tc Susceptometer to Monitor Transfusional Iron Overload NCT01241357 | Columbia University | — |
| Completed | Mesenchymal Stem Cells in the Treatment of Relapsed/Refractory Severe Acquired Aplastic Anemia NCT01297972 | University of Sao Paulo | Phase 1 / Phase 2 |
| Unknown | Mesenchymal Stem Cells Transplantation to Patients With Relapsed/Refractory Aplastic Anemia. NCT01305694 | Guangzhou General Hospital of Guangzhou Military Command | Phase 1 / Phase 2 |
| Active Not Recruiting | Infection Prophylaxis and Management in Treating Cytomegalovirus (CMV) Infection in Patients With Hematologic NCT01199562 | City of Hope Medical Center | — |
| Unknown | Safety and Efficacy Study of Umbilical Cord/Placenta-Derived Mesenchymal Stem Cells to Treat Severe Aplastic A NCT01182662 | Shandong University | Phase 2 |
| Completed | A Pilot Study of Fludarabine Plus Cyclophosphamide in Refractory Severe Aplastic Anemia NCT01187017 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 1 / Phase 2 |
| Completed | Cyclophosphamide Plus Cyclosporine in Treatment-Naive Severe Aplastic Anemia NCT01193283 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 1 / Phase 2 |
| Completed | Bone Marrow Transplantation of Patients in Remission Using Partially Matched Relative Donor NCT01350245 | Sidney Kimmel Comprehensive Cancer Center at Thomas Jefferson University | Phase 2 |
| Unknown | Comparison of Cy-Atg vs Flu-Atg for the Conditioning Therapy in Allo-HCT for Adult Aplastic Anemia NCT01145976 | Cooperative Study Group A for Hematology | Phase 3 |
| Completed | Hematopoietic Stem Cell Transplantation for the Treatment of Patients With Fanconi Anemia Lacking a Genotypica NCT00987480 | Memorial Sloan Kettering Cancer Center | Phase 2 |
| Completed | Human Leukocyte Antigen (HLA)-Haploidentical Hematopoietic Stem Cell Transplantation for Patients With Aplasti NCT01105273 | Asan Medical Center | Phase 1 / Phase 2 |
| Withdrawn | Collection of Blood and Bone Marrow From Patients With Aplastic Anemia for Analysis of Adhesion Molecules, Che NCT01680055 | Shandong University | — |
| Completed | Fludarabine Phosphate, Melphalan, Total-Body Irradiation, Donor Stem Cell Transplant in Treating Patients With NCT00856388 | Roswell Park Cancer Institute | N/A |
| Unknown | Study of Fludarabine + Cyclophosphamide + TBI Conditioning Regimen for Double Units Cord Blood Transplantation NCT00881933 | The Korean Society of Pediatric Hematology Oncology | Phase 1 / Phase 2 |
| Unknown | Reduced Toxicity Fludarabine (Flu) + Cyclophosphamide (CPM) + Rabbit Antithymocyte Globulin (rATG) Conditionin NCT00882323 | The Korean Society of Pediatric Hematology Oncology | Phase 2 |
| Completed | Neuropsychological Effects of Immunosuppressive Treatment in Subjects With Aplastic Anemia NCT00767650 | National Heart, Lung, and Blood Institute (NHLBI) | — |
| Completed | Rabbit Antithymocyte Globulin (Thymoglobuline) With Ciclosporin for Patients With Acquired Aplastic Anaemia NCT00471848 | European Society for Blood and Marrow Transplantation | Phase 2 |
| Terminated | Treatment of Menorrhagia in Women With Thrombocytopenia Using Platelets or Platelets and Hormones NCT00556400 | Eunice Kennedy Shriver National Institute of Child Health and Human Development (NICHD) | Phase 1 / Phase 2 |
| Completed | Investigation of the Cylex® ImmuKnow® Assay NCT00569842 | Indiana University School of Medicine | — |
| Completed | Unrelated Cord Blood Transplant Plus a Haplo-Identical (Half-Matched), T-Cell Depleted Stem Transplant From a NCT00673114 | Joanne Kurtzberg, MD | Phase 1 / Phase 2 |
| Completed | Stem Cell Transplant (SCT) for Dyskeratosis Congenita or SAA NCT00455312 | Masonic Cancer Center, University of Minnesota | Phase 2 / Phase 3 |
| Completed | Cyclophosphamide and Anti-thymocyte Globulin Followed By Methotrexate and Cyclosporine in Preventing Chronic G NCT00343785 | Fred Hutchinson Cancer Center | Phase 2 |
| Terminated | Cyclophosphamide, Antithymocyte Globulin, and Total-Body Irradiation in Treating Patients With Severe Aplastic NCT00354419 | Fred Hutchinson Cancer Center | Phase 1 |
| Terminated | A Phase II Study of Umbilical Cord Blood Transplantation NCT00676806 | Tufts Medical Center | Phase 2 |
| Completed | Thymoglobulin and Cyclosporine in Patients With Aplastic Anemia or Myelodysplastic Syndrome NCT00806598 | M.D. Anderson Cancer Center | Phase 2 |
| Completed | Anti-thymocyte Globulin and Cyclosporine as First-Line Therapy in Treating Patients With Severe Aplastic Anemi NCT01231841 | The Cleveland Clinic | Phase 2 |
| Unknown | Safety Study of CD3/CD19 Depleted Haploidentical Stem Cells NCT01919866 | University Children's Hospital Tuebingen | Phase 1 / Phase 2 |
| Completed | Rabbit Antithymocyte Globulin Versus Campath-1H for Treating Severe Aplastic Anemia NCT00065260 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 2 |
| Completed | Multi Center Case Control Study on Multiple Risk Factors of Aplastic Anemia NCT03208647 | Shengyun Lin | — |
| Completed | Purified CD34+ Hematopoietic Stem Cell Transplantation From Alternate Donors for Patients With Severe Aplastic NCT00186797 | St. Jude Children's Research Hospital | N/A |
| Completed | Nonmyeloablative Allogeneic Stem Cell Transplantation From HLA-Matched Unrelated Donor for the Treatment of He NCT00533923 | Beth Israel Deaconess Medical Center | Phase 2 |
| Terminated | Allogeneic Stem Cell Transplant for Patients With Severe Aplastic Anemia NCT00578903 | Baylor College of Medicine | Phase 2 |
| Completed | NMA Allogeneic Hematopoietic Cell Transplant in Hematologic Cancer/Disorders NCT00053989 | Roswell Park Cancer Institute | Phase 2 |
| Completed | Nonmyeloablative Allogeneic Transplant NCT01272817 | Scripps Health | N/A |
| Completed | Non-Myeloablative Allogeneic Stem Cell Transplantation With Matched Unrelated Donors for Treatment of Hematolo NCT00513175 | University of California, San Francisco | — |
| Unknown | Study of Allogeneic Bone Marrow and T-Cell Depleted, CD34+ Peripheral Blood Stem Cell Transplantation in Patie NCT00017654 | Northwestern Memorial Hospital | N/A |
| Completed | Stem Cell Mobilization Potential in Patients With Aplastic Anemia in Remission NCT00011830 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 1 |
| Completed | Purine Analog-Based Conditioning in Patients With Severe Aplastic Anemia NCT00427336 | M.D. Anderson Cancer Center | N/A |
| Completed | Mycophenolate Mofetil and Cyclosporine to Treat Relapsing Aplastic Anemia NCT00005935 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 2 |
| Completed | Oral Manifestations of Aplastic Anemia NCT00006300 | National Institute of Dental and Craniofacial Research (NIDCR) | — |
| Completed | Fludarabine Based Conditioning for Allogeneic Transplantation for Advanced Hematologic Malignancies NCT01499147 | University of Illinois at Chicago | N/A |
| Terminated | A Study to Determine Whether Therapy With Daclizumab Will Benefit Patients With Bone Marrow Failure NCT00001962 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 2 |
| Completed | Nonmyeloablative Allo SCT for the Treatment of Hematologic Disorders NCT00636909 | Beth Israel Deaconess Medical Center | Phase 2 |
| Completed | Phase III Randomized Study of Cyclophosphamide With or Without Antithymocyte Globulin Before Bone Marrow Trans NCT00004474 | Roswell Park Cancer Institute | Phase 3 |
| Completed | Protection Against Benzene Toxicity NCT00011453 | National Institute of Environmental Health Sciences (NIEHS) | — |
| Terminated | Blood Transplantation for Patients With Hematologic Malignancies or Bone Marrow Failure States NCT00038779 | M.D. Anderson Cancer Center | N/A |
| Completed | Study of High Dose Cyclophosphamide in Patients With Severe Aplastic Anemia and Paroxysmal Nocturnal Hemoglobi NCT00004464 | Sidney Kimmel Comprehensive Cancer Center at Johns Hopkins | Phase 2 |
| Completed | Phase II Study of Bone Marrow Transplantation Using Related Donors in Patients With Aplastic Anemia NCT00004323 | National Center for Research Resources (NCRR) | Phase 2 |
| Completed | Stem Cell Factor Medication for Aplastic Anemia NCT00001398 | National Heart, Lung, and Blood Institute (NHLBI) | Phase 1 |
| No Longer Available | Expanded Access Use of Itacitinib to Treat a Single Patient With Aplastic Anemia NCT03906318 | Incyte Corporation | — |