Trials / Conditions / Spinal Muscular Atrophy (SMA)

Spinal Muscular Atrophy (SMA)

27 registered clinical trials studyying Spinal Muscular Atrophy (SMA) — 20 currently recruiting.

Status	Trial	Sponsor	Phase
Not Yet Recruiting	Neuroproprioceptive Equine-Assisted Physiotherapy for Spinal Muscular Atrophy NCT07336602	Charles University, Czech Republic	N/A
Recruiting	HABIT-ILE + FST in Children With SMA: Preliminary Effectiveness NCT07488338	Teachers College, Columbia University	N/A
Not Yet Recruiting	Self-Efficacy Enhancement Using a Multicomponent Support Group for Caregivers of Children With DMD/SMA NCT07356063	Aga Khan University	N/A
Recruiting	Assessment of a Portable Digital Device for Quantified Analysis of Markerless Walking in Volunteers With Neuro NCT07321977	Institut de Myologie, France	N/A
Recruiting	A Study to Assess the Safety, Tolerability, Efficacy, Pharmacokinetics, and Immunogenicity of Intravenous Admi NCT07287982	argenx	Phase 2
Recruiting	Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or S NCT07286565	Centre Hospitalier Universitaire de Liege	N/A
Not Yet Recruiting	Psychological Evaluation of the Parental Experience of Newborn Screening for Infantile Spinal Muscular Atrophy NCT07208903	University Hospital, Strasbourg, France	—
Recruiting	Real World Clinical Effectiveness & Safety of Vesemnogene Lantuparvovec for Spinal Muscular Atrophy (SMA) in L NCT07265232	Lantu Biopharma	Phase 3
Recruiting	Diagnostic Journey, Patient Experience, and Disparities in the Treatment of Spinal Muscular Atrophy (SMA) in t NCT07223489	Medstar Health Research Institute	—
Enrolling By Invitation	The Use of Assistive Gait Devices Can Reduce the Risk of Falls in Patients With Neuromuscular Diseases Followi NCT07072676	LMU Klinikum	N/A
Recruiting	Safety and Tolerability of Low Motoneuron Stimulation Via Transcranial Magnetic Stimulation in Spinal Muscular NCT06977269	Charitable Foundation Children with Spinal Muscular Atrophy	N/A
Recruiting	Long Read Analysis in Spinal Muscular Atrophy - LOREASI NCT07332702	University Hospital, Rouen	N/A
Enrolling By Invitation	Clinical Trial to Assess the Safety and Efficacy of EXG001-307 in Patients With Spinal Muscular Atrophy NCT06888661	Guangzhou Jiayin Biotech Ltd	EARLY_Phase 1
Recruiting	Robot-assisted Training NCT06648486	Peking University Third Hospital	N/A
Active Not Recruiting	Ultrasonographic Muscle Assessment and Functional Scales in Spinal Muscular Atrophy NCT06599606	Istanbul University - Cerrahpasa	—
Recruiting	The Effect of a Muscle-mimicking, Fabric-type Shoulder Orthosis on Functional Movements of the Upper Limb in P NCT06363357	Seoul National University Hospital	N/A
Terminated	Gut Peptides and Bone Remodeling in Children With Neuromuscular Disorders NCT07254988	University of Copenhagen	N/A
Recruiting	Study of the Safety and Efficacy of an Adeno-Associated Viral Vector Carrying the SMN Gene After a Single Intr NCT05747261	Biocad	Phase 1 / Phase 2
Recruiting	Long-term Follow-up of Patients With Spinal Muscular Atrophy Treated With OAV101 in Clinical Trials NCT05335876	Novartis Pharmaceuticals	Phase 3
Recruiting	Adult SMA Research and Clinical Hub NCT06978985	Newcastle-upon-Tyne Hospitals NHS Trust	—
Active Not Recruiting	A Study to Investigate the Safety and Efficacy of RO7204239 in Combination With Risdiplam (RO7034067) in Parti NCT05115110	Hoffmann-La Roche	Phase 2 / Phase 3
Completed	Virtual Reality for the Mitigation of Anxiety During Intrathecal Administration in Participants With Spinal Mu NCT05354414	Biogen	N/A
Terminated	Effect of Low-Dose Celecoxib on SMN2 in Patients With Spinal Muscular Atrophy NCT02876094	Hugh McMillan	Phase 2
Recruiting	Registry of Patients With a Diagnosis of Spinal Muscular Atrophy (SMA) NCT04174157	Novartis Pharmaceuticals	—
Recruiting	Observational Study to Observe Variations of Gait Parameters in Patients With Neuromuscular Diseases NCT06666816	IRCCS Eugenio Medea	—
Completed	Spinal Muscular Atrophy (SMA) Biomarkers Study in the Immediate Postnatal Period of Development NCT01736553	Ohio State University	—
Withdrawn	Multi-disease Carrier Screening Test Validation NCT01663584	Natera, Inc.	—