| Not Yet Recruiting | DMD and Gamified Physiotherapy NCT07368400 | Başak Çağla Arslan | N/A |
| Not Yet Recruiting | Invasive Home Ventilation in Denmark NCT07467187 | Rigshospitalet, Denmark | — |
| Not Yet Recruiting | Registry for Duchenne and Becker Muscular Dystrophy NCT07402122 | Dr. Andreas Ziegler | — |
| Not Yet Recruiting | A Study to Evaluate the Safety and Tolerability of Rituxan in Duchenne Muscular Dystrophy NCT07475754 | Peking Union Medical College Hospital | N/A |
| Recruiting | Urinary Titin Biomarker in DMD NCT07332013 | Children's Hospital of Philadelphia | N/A |
| Not Yet Recruiting | A Remote Study Using Technology to Assess Outcomes in DMD NCT07423026 | University of Oxford | — |
| Not Yet Recruiting | Self-Efficacy Enhancement Using a Multicomponent Support Group for Caregivers of Children With DMD/SMA NCT07356063 | Aga Khan University | N/A |
| Not Yet Recruiting | The Baby Duchenne Study: Characterizing Developmental and Clinical Outcomes in the First Three Years in Childr NCT07092540 | University of Rochester | — |
| Not Yet Recruiting | Factors Influencing Physical Activity Levels in Children With Duchenne Muscular Dystrophy: An ICF-CY-Based Stu NCT07369609 | Hacettepe University | — |
| Not Yet Recruiting | Sodium/Glucose Cotransporter-2 Inhibitors (SGLT2i) Therapy in Duchenne Cardiomyopathy NCT07172971 | Larry W. Markham | Phase 1 |
| Recruiting | DMD Gene Variants and Cardiac Dysfunction in Young Males With Dystrophinopathies NCT07515235 | Aristotle University Of Thessaloniki | — |
| Enrolling By Invitation | The Effect of Dual-tasking Program on Cognitive and Physical Functions and Independence in Activities of Daily NCT06887491 | Lokman Hekim University | N/A |
| Active Not Recruiting | A Trial to Investigate the Safety and Pharmacokinetics of GRT6019 in Healthy Male Participants NCT07347548 | Grünenthal GmbH | Phase 1 |
| Active Not Recruiting | A Study to Evaluate the Safety and Tolerability of RAG-18 in Pediatric Patients With Duchenne Muscular Dystrop NCT07282652 | Peking Union Medical College Hospital | EARLY_Phase 1 |
| Recruiting | Active NBS Study: Decentralised Monitoring Motor Development in Children With Duchenne Muscular Dystrophy or S NCT07286565 | Centre Hospitalier Universitaire de Liege | N/A |
| Completed | A Trial to Investigate Safety and Pharmacokinetics of GRT6019, Including Food Effect, in Healthy Male Particip NCT07317063 | Grünenthal GmbH | Phase 1 |
| Enrolling By Invitation | Duchenne Muscular Dystrophy and the Viscoelastic Properties of Upper Limb Muscles NCT07435116 | Sanko University | — |
| Recruiting | A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 45 Skipping to Evaluate the Safety a NCT07038824 | Entrada Therapeutics, Inc. | Phase 1 / Phase 2 |
| Enrolling By Invitation | A Long-term Follow-up Study for Participants That Completed the SAT-3247-CL-101 Study NCT06867107 | Satellos Bioscience, Inc. | Phase 2 |
| Not Yet Recruiting | The Effect of Virtual Reality Applications on Upper Extremity Functions in Patients With Duchenne Muscular Dys NCT07039799 | Istanbul University | N/A |
| Recruiting | Safety and Dystrophin Expression of SPOT-mRNA03 in Duchenne Muscular Dystrophy (DMD) Patients NCT07188012 | Shanghai Siponuoyin Biotechnology Co Ltd | EARLY_Phase 1 |
| Recruiting | Fear of Falling in Muscular Dystrophy NCT07129954 | Universita di Verona | N/A |
| Recruiting | A Study in Participants With Duchenne Muscular Dystrophy Amenable to Exon 44 Skipping to Evaluate the Safety a NCT07037862 | Entrada Therapeutics, Inc. | Phase 1 / Phase 2 |
| Completed | Virtual Reality and Whole Body Vibration on Muscle Strength and Balance in Children With DMD NCT07338812 | Cairo University | N/A |
| Recruiting | DMD Voice: Qualitative Interviews With Patients and Caregivers NCT06925269 | Red Nucleus Enterprise Solutions, LLC | — |
| Recruiting | Research on the Relationship Between Scoliosis, Pain, Quality of Life, and Trunk Muscle Compensation Patterns NCT06755138 | Seoul National University Hospital | — |
| Withdrawn | A Study of PGN-EDO51 or Placebo in People With Duchenne Muscular Dystrophy Amenable to Exon 51-Skipping Treatm NCT06833931 | PepGen Inc | Phase 2 |
| Recruiting | Follow-up of NIV At Home in Patients with Duchenne Muscular Dystrophy NCT06773988 | Universitaire Ziekenhuizen KU Leuven | — |
| Not Yet Recruiting | Effects of Lumbopelvic Stabilization-based Physiotherapy and Rehabilitation Training in Duchenne Muscular Dyst NCT06643923 | Lokman Hekim University | N/A |
| Completed | Nutritional Status and Therapy in DMD Patients NCT06682585 | Ankara University | N/A |
| Recruiting | Evaluation of the Safety, Tolerability, and Efficacy of LE051 in Patients With Duchenne Muscular Dystrophy NCT06900049 | Shanghai Jiao Tong University School of Medicine | EARLY_Phase 1 |
| Completed | Relation Between Muscle Architecture and Functional Ability in Children With Duchenne Muscular Dystrophy NCT07437378 | Deraya University | — |
| Recruiting | Evaluation of the Safety and Efficacy of BBM-D101 to Treat Patients with Duchenne Muscular Dystrophy NCT06641895 | Shanghai Jiao Tong University School of Medicine | EARLY_Phase 1 |
| Active Not Recruiting | A Study to Evaluate the Safety and Tolerability of GEN6050X in Duchenne Muscular Dystrophy. NCT06392724 | Peking Union Medical College Hospital | EARLY_Phase 1 |
| Recruiting | Establishing Walking-related Digital Biomarkers in Rare Childhood Onset Progressive Neuromuscular Disorders NCT06839469 | Columbia University | — |
| Terminated | Gut Peptides and Bone Remodeling in Children With Neuromuscular Disorders NCT07254988 | University of Copenhagen | N/A |
| Active Not Recruiting | Safety, Tolerability, Pharmacodynamic, Efficacy, and Pharmacokinetic Study of DYNE-251 in Participants With Du NCT05524883 | Dyne Therapeutics | Phase 1 / Phase 2 |
| Completed | Peabody Developmental Motor Scaling In Children With Period Duchenne Muscular Dystrophy NCT05990608 | Ondokuz Mayıs University | — |
| Active Not Recruiting | Extension Study of NS-089/NCNP-02 in DMD NCT05135663 | Nippon Shinyaku Co., Ltd. | Phase 2 |
| Unknown | E-monitoring of PULMonary Function in Patients With Duchenne Muscular Dystrophy at Home" NCT05516745 | Medical University of Gdansk | N/A |
| Terminated | A Study to Assess the Safety, Tolerability and Preliminary Efficacy of ASP0367 (MA-0211) in Pediatric Male Par NCT04184882 | Astellas Pharma Inc | Phase 1 |
| Completed | Twice Weekly Steroids and Exercise as Therapy for DMD NCT04322357 | University of Florida | Phase 2 |
| Terminated | A Low Interventional Study to Monitor Activity Using Wearable Sensors in Duchenne Muscular Dystrophy NCT04254172 | Pfizer | — |
| Terminated | A Phase III Double-blind Study With Idebenone in Patients With Duchenne Muscular Dystrophy (DMD) Taking Glucoc NCT02814019 | Santhera Pharmaceuticals | Phase 3 |
| Unknown | The Safety, Efficacy and Tolerability of Remote Ischemic Preconditioning as a Therapy to DMD NCT02614820 | General Hospital of Chinese Armed Police Forces | N/A |
| Completed | Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy NCT02420379 | Sarepta Therapeutics, Inc. | Phase 2 |
| Completed | Study of Eteplirsen in DMD Patients NCT02255552 | Sarepta Therapeutics, Inc. | Phase 3 |
| Withdrawn | A Trial of Chronotherapy of Corticosteroids in Duchenne Muscular Dystrophy NCT02036463 | Ann & Robert H Lurie Children's Hospital of Chicago | Phase 2 |
| Completed | A Study to Assess Safety/Tolerability, pk, Effects on Histology, Clinical Parameters of Givinostat in Children NCT01761292 | Italfarmaco | Phase 1 / Phase 2 |
| Completed | Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy NCT01540409 | Sarepta Therapeutics, Inc. | Phase 2 |
| Completed | To Compare the Pharmacokinetics Profiles of ISO 20, IBU 200 and IBU Plus ISO Combinations 200 + 20 NCT01478022 | Parent Project, Italy | Phase 1 |
| Completed | Research of Biomarkers in Duchenne Muscular Dystrophy Patients NCT01380964 | Genethon | — |
| Completed | Cardiomyopathy in DMD: Lisinopril vs. Losartan NCT01982695 | Nationwide Children's Hospital | N/A |
| Completed | Efficacy and Tolerability of Idebenone in Boys With Cardiac Dysfunction Associated With Duchenne Muscular Dyst NCT00654784 | Santhera Pharmaceuticals | Phase 2 |