| Not Yet Recruiting | A First-in-human Study of the Effects of SRP-1005 in Participants With Huntington's Disease Huntington's Disease | Phase 1 | 2026-05-05 |
| Withdrawn | A Study of SRP-9005 in Limb Girdle Muscular Dystrophy Type 2C/R5 Pediatric and Adult Participants Muscular Dystrophies, Limb-Girdle | Phase 3 | 2025-06-30 |
| Terminated | Study to Evaluate the Safety, Tolerability, and Efficacy of SRP-9004 Administered by Systemic Infusion in Limb Limb Girdle Muscular Dystrophy, Limb Girdle Muscular Dystrophy Type 2D/R3 | Phase 1 | 2025-01-09 |
| Terminated | A Gene Transfer Therapy to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) Followi Duchenne Muscular Dystrophy | Phase 1 | 2024-09-18 |
| Enrolling By Invitation | An Observational Study Comparing Delandistrogene Moxeparvovec With Standard of Care in Participants With Duche Duchenne Muscular Dystrophy | — | 2024-02-07 |
| Terminated | A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) F Duchenne Muscular Dystrophy | Phase 1 | 2024-01-29 |
| Active Not Recruiting | A Trial to Learn More About an Experimental Gene Therapy Called Bidridistrogene Xeboparvovec (SRP-9003) as a P Limb-girdle Muscular Dystrophy | Phase 3 | 2024-01-15 |
| Enrolling By Invitation | A Long-term Follow-up Study of Participants Who Received Delandistrogene Moxeparvovec (SRP-9001) in a Previous Duchenne Muscular Dystrophy | Phase 3 | 2023-09-27 |
| Active Not Recruiting | A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) i Duchenne Muscular Dystrophy | Phase 3 | 2023-05-31 |
| Terminated | A Gene Transfer Study to Evaluate the Safety, Tolerability and Efficacy of SRP-6004 in Ambulatory Participants Limb Girdle Muscular Dystrophy | Phase 1 | 2023-05-22 |
| Active Not Recruiting | A Gene Transfer Single Dose Study to Evaluate the Safety, Tolerability and Efficacy of SRP-9003 in Non-Ambulat Limb Girdle Muscular Dystrophy | Phase 1 | 2022-12-19 |
| Completed | A Gene Transfer Therapy Study to Evaluate the Safety and Efficacy of Delandistrogene Moxeparvovec (SRP-9001) i Duchenne Muscular Dystrophy | Phase 3 | 2021-10-27 |
| Active Not Recruiting | A Study of the Natural History of Participants With LGMD2E/R4, LGMD2D/R3, LGMD2C/R5, and LGMD2A/R1 ≥ 4 Years o Limb-girdle Muscular Dystrophy | — | 2021-04-22 |
| Recruiting | A Gene Transfer Therapy Study to Evaluate the Safety of and Expression From Delandistrogene Moxeparvovec (SRP- Muscular Dystrophy, Duchenne | Phase 1 | 2020-11-23 |
| Active Not Recruiting | A Study to Compare Safety and Efficacy of High Doses of Eteplirsen in Participants With Duchenne Muscular Dyst Muscular Dystrophy, Duchenne | Phase 3 | 2020-07-13 |
| Terminated | Two-Part Study for Dose Determination of Vesleteplirsen (SRP-5051) (Part A), Then Dose Expansion (Part B) in P Duchenne Muscular Dystrophy | Phase 2 | 2019-06-26 |
| Terminated | A Study to Evaluate Safety, Tolerability, and Efficacy of Eteplirsen in Participants With Duchenne Muscular Dy Duchenne Muscular Dystrophy | Phase 2 | 2019-06-26 |
| Enrolling By Invitation | A Long-term Observational Study Evaluating Eteplirsen, Golodirsen, or Casimersen in Routine Clinical Practice Duchenne Muscular Dystrophy | — | 2019-01-07 |
| Terminated | An Open-Label Extension Study for Patients With Duchenne Muscular Dystrophy Who Participated in Studies of SRP Muscular Dystrophy, Duchenne | Phase 1 / Phase 2 | 2018-12-19 |
| Completed | A Randomized, Double-blind, Placebo-controlled Study of Delandistrogene Moxeparvovec (SRP-9001) for Duchenne M Muscular Dystrophy, Duchenne | Phase 1 / Phase 2 | 2018-12-05 |
| Terminated | Gene Delivery Clinical Trial of SRP-9003 (Bidridistrogene Xeboparvovec) for Participants With Limb-Girdle Musc Limb-Girdle Muscular Dystrophy, Type 2E | Phase 1 / Phase 2 | 2018-10-27 |
| Terminated | An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy Duchenne Muscular Dystrophy | Phase 3 | 2018-08-02 |
| Completed | A Study to Evaluate the Safety, Tolerability, and Pharmacokinetics of a Single Dose of SRP-5051 (Vesleteplirse Muscular Dystrophy, Duchenne | Phase 1 | 2018-02-05 |
| Completed | A Gene Transfer Therapy Study to Evaluate the Safety of Delandistrogene Moxeparvovec (SRP-9001) in Participant Duchenne Muscular Dystrophy | Phase 1 / Phase 2 | 2018-01-04 |
| Completed | Study of Eteplirsen in Young Participants With Duchenne Muscular Dystrophy (DMD) Amenable to Exon 51 Skipping Duchenne Muscular Dystrophy | Phase 2 | 2017-08-16 |
| Completed | Study of SRP-4045 (Casimersen) and SRP-4053 (Golodirsen) in Participants With Duchenne Muscular Dystrophy (DMD Duchenne Muscular Dystrophy | Phase 3 | 2016-09-28 |
| Completed | rAAVrh74.MHCK7.DYSF.DV for Treatment of Dysferlinopathies Dysferlinopathy | Phase 1 | 2016-03-01 |
| Completed | Dose-Titration and Open-label Extension Study of SRP-4045 in Advanced Stage Duchenne Muscular Dystrophy (DMD) Duchenne Muscular Dystrophy | Phase 1 | 2015-10-08 |
| Completed | Safety Study of Eteplirsen to Treat Early Stage Duchenne Muscular Dystrophy Duchenne Muscular Dystrophy (DMD) | Phase 2 | 2015-06-30 |
| Completed | A Gene Transfer Therapy Study to Evaluate the Safety of SRP-9004 (Patidistrogene Bexoparvovec) in Participants Limb-Girdle Muscular Dystrophy, Type 2D | Phase 1 / Phase 2 | 2015-02-01 |
| Completed | Phase I/II Study of SRP-4053 in DMD Patients Duchenne Muscular Dystrophy | Phase 1 / Phase 2 | 2015-01-13 |
| Completed | Study of Eteplirsen in DMD Patients Duchenne Muscular Dystrophy (DMD) | Phase 3 | 2014-11-17 |
| Completed | Safety Study of Eteplirsen to Treat Advanced Stage Duchenne Muscular Dystrophy Muscular Dystrophy, Duchenne | Phase 2 | 2014-11-01 |
| Completed | A Study to Assess the Safety, Tolerability and Pharmacokinetics of AVI-7288 in Healthy Adult Volunteers Marburg Hemorrhagic Fever | Phase 1 | 2013-05-01 |
| Withdrawn | A Study to Assess the Safety, Tolerability and Pharmacokinetics of AVI-7537 in Healthy Adult Volunteers Ebola Hemorrhagic Fever | Phase 1 | 2012-08-01 |
| Completed | Efficacy, Safety, and Tolerability Rollover Study of Eteplirsen in Subjects With Duchenne Muscular Dystrophy Duchenne Muscular Dystrophy (DMD) | Phase 2 | 2012-02-27 |
| Completed | Efficacy Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy Patients Duchenne Muscular Dystrophy | Phase 2 | 2011-07-01 |
| Terminated | Safety Study of Single Administration Intravenous Treatment for Influenza Influenza | Phase 1 | 2011-06-01 |
| Completed | Safety Study of Single Administration Post-exposure Prophylaxis Treatment for Marburg Virus Marburg Hemorrhagic Fever | Phase 1 | 2011-05-01 |
| Completed | Safety Study of Single Administration Post-Exposure Prophylaxis Treatment for Ebola Virus Ebola Hemorrhagic Fever | Phase 1 | 2010-05-01 |
| Completed | Dose-Ranging Study of AVI-4658 to Induce Dystrophin Expression in Selected Duchenne Muscular Dystrophy (DMD) P Duchenne Muscular Dystrophy | Phase 1 / Phase 2 | 2009-01-01 |
| Terminated | Safety and Efficacy Study of AVI-5126 When Used on Vein Grafts Before Use in Heart by-Pass Graft Surgery (CABG Cardiovascular Disease, Coronary Artery Bypass | Phase 2 | 2007-03-01 |
| Completed | Pharmacokinetic Study in Cerebral Spinal Fluid After a Single Dose of AVI-4020 West Nile Virus | Phase 1 | 2006-10-01 |
| Completed | Pharmacokinetic Study of a Single Dose of AVI-4065 in Cerebral Spinal Fluid Encephalitis | Phase 1 | 2006-09-01 |
| Completed | Pharmacokinetic Study of a Single Dose of AVI-4126 (RESTEN-NG®) in Cerebral Spinal Fluid Neoplasms | Phase 1 | 2006-06-01 |
| Terminated | Study of AVI-4065 in Healthy Volunteers and Chronic Active HCV Patients Hepatitis C | Phase 1 / Phase 2 | 2005-09-01 |
| Completed | Safety and Efficacy of RESTEN-MP When Used in Conjunction With a Bare Metal Stent in Coronary Arteries Coronary Artery Disease, Coronary Restenosis | Phase 2 | 2005-09-01 |
| Terminated | An Exploratory Study of AVI-4020 in Patients With Possible Acute Neuroinvasive West Nile Virus (WNV) Disease West Nile Fever | Phase 1 | 2004-11-01 |
| Terminated | A Phase 1b Study Evaluating RESTEN-MP in Subjects With Focal de Novo Stenosis Coronary Artery Disease, Coronary Stent Restenosis | Phase 1 | 2003-08-01 |