Clinical Trials Directory

Trials / Terminated

TerminatedNCT03532542

An Extension Study to Evaluate Casimersen or Golodirsen in Patients With Duchenne Muscular Dystrophy

Long-term, Open-label Extension Study for Patients With Duchenne Muscular Dystrophy Enrolled in Clinical Trials Evaluating Casimersen or Golodirsen

Status
Terminated
Phase
Phase 3
Study type
Interventional
Enrollment
171 (actual)
Sponsor
Sarepta Therapeutics, Inc. · Industry
Sex
Male
Age
7 Years – 23 Years
Healthy volunteers
Not accepted

Summary

The main objective of this study is to evaluate the safety and tolerability of long-term treatment with casimersen or golodirsen in patients with Duchenne muscular dystrophy (DMD).

Conditions

Interventions

TypeNameDescription
DRUGCasimersenCasimersen solution for IV infusion
DRUGGolodirsenGolodirsen solution for IV infusion

Timeline

Start date
2018-08-02
Primary completion
2023-07-26
Completion
2023-07-26
First posted
2018-05-22
Last updated
2024-09-19
Results posted
2024-09-19

Locations

50 sites across 13 countries: United States, Belgium, Bulgaria, Canada, Czechia, France, Germany, Israel, Italy, Poland, Spain, Sweden, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT03532542. Inclusion in this directory is not an endorsement.