Genethon

Academic / Other · 13 registered clinical trials — 3 currently recruiting.

Status	Trial	Phase	Started
Recruiting	Efficacy and Safety of GNT0003 Following Imlifidase Pre-treatment in Severe Crigler-Najjar Syndrome Crigler-Najjar Syndrome	Phase 2	2024-11-08
Completed	Natural History Study of Patients With Limb-Girdle Muscular Dystrophy 2I LGMD2I	—	2020-02-19
Recruiting	Natural History of Duchenne Muscular Dystrophy Duchenne Muscular Dystrophy	—	2019-12-19
Recruiting	Gene Therapy for Severe Crigler Najjar Syndrome Crigler-Najjar Syndrome	N/A	2018-03-19
Completed	Immunity Against AAV in Crigler Najjar Patient Crigler Najjar Syndrome	—	2014-11-01
Active Not Recruiting	Long Term Safety Follow up of Haematopoietic Stem Cell Gene Therapy for the Wiskott Aldrich Syndrome Wiskott-Aldrich Syndrome	Phase 1 / Phase 2	2014-09-01
Terminated	Gene Therapy for X-linked Chronic Granulomatous Disease X-Linked Chronic Granulomatous Disease	Phase 1 / Phase 2	2013-06-24
Terminated	Gene Therapy for X-linked Chronic Granulomatous Disease (X-CGD) X-Linked Chronic Granulomatous Disease	Phase 1 / Phase 2	2013-06-24
Unknown	Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping Duchenne Muscular Dystrophy	—	2011-10-01
Completed	Research of Biomarkers in Duchenne Muscular Dystrophy Patients Duchenne Muscular Dystrophy (DMD)	—	2011-06-01
Completed	Gene Therapy for WAS Wiskott-Aldrich Syndrome	Phase 1 / Phase 2	2011-05-01
Completed	Gene Therapy for Wiskott-Aldrich Syndrome (WAS) Wiskott-Aldrich Syndrome	Phase 1 / Phase 2	2011-03-01
Completed	Clinical Study of AAV1-gamma-sarcoglycan Gene Therapy for Limb Girdle Muscular Dystrophy Type 2C Limb Girdle Muscular Dystrophy Type 2C, Gamma-sarcoglycanopathy	Phase 1	2006-11-01