Trials / Unknown
UnknownNCT01385917
Observational Study of Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping
Study of Clinical and Radiological Changes in Patients With Duchenne Muscular Dystrophy Theoretically Treatable With Exon 53 Skipping
- Status
- Unknown
- Phase
- —
- Study type
- Observational
- Enrollment
- 45 (estimated)
- Sponsor
- Genethon · Academic / Other
- Sex
- Male
- Age
- 12 Years – 20 Years
- Healthy volunteers
- Not accepted
Summary
PreU7-53 is a natural history study. The objective is to monitor the clinical and radiological course of upper limb muscle impairment in patients with Duchenne Muscular Dystrophy (DMD), potentially treatable with AAV-mediated exon 53 skipping.
Conditions
Timeline
- Start date
- 2011-10-01
- Primary completion
- 2018-12-01
- Completion
- 2018-12-01
- First posted
- 2011-06-30
- Last updated
- 2016-04-12
Locations
2 sites across 2 countries: France, United Kingdom
Source: ClinicalTrials.gov record NCT01385917. Inclusion in this directory is not an endorsement.