Clinical Trials Directory

Trials / Conditions / Lafora Disease

Lafora Disease

4 registered clinical trials studyying Lafora Disease1 currently recruiting.

StatusTrialSponsorPhase
RecruitingA Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease
NCT06609889
Berge MinassianPhase 1 / Phase 2
CompletedNatural History and Functional Status Study of Patients With Lafora Disease
NCT03876522
Ionis Pharmaceuticals, Inc.
CompletedKetogenic Diet in Lafora Disease
NCT00007124
National Institute of Neurological Disorders and Stroke (NINDS)
AvailableIntravenous VAL-1221 Lafora Expanded Access Protocol
NCT05930223
Parasail, LLC