Trials / Completed
CompletedNCT03876522
Natural History and Functional Status Study of Patients With Lafora Disease
Prospective, Longitudinal, Observational Study of the Natural History and Functional Status of Patients With Lafora Disease
- Status
- Completed
- Phase
- —
- Study type
- Observational
- Enrollment
- 33 (actual)
- Sponsor
- Ionis Pharmaceuticals, Inc. · Industry
- Sex
- All
- Age
- 5 Years
- Healthy volunteers
- Not accepted
Summary
A natural history and functional status study to characterize the clinical disease course in Lafora disease patients using standardized, quantitative evaluations and to identify useful biomarkers and clinical outcome measures for use in future Lafora treatment studies.
Conditions
Timeline
- Start date
- 2019-01-09
- Primary completion
- 2022-04-01
- Completion
- 2022-04-01
- First posted
- 2019-03-15
- Last updated
- 2022-09-28
Locations
4 sites across 3 countries: United States, Italy, Spain
Source: ClinicalTrials.gov record NCT03876522. Inclusion in this directory is not an endorsement.