Clinical Trials Directory

Trials / Sponsors / Berge Minassian

Berge Minassian

Academic / Other · 1 registered clinical trial1 currently recruiting.

StatusTrialPhaseStarted
RecruitingA Safety and Efficacy of Intrathecally Administered ION283 in Patients With Lafora Disease
Lafora Disease
Phase 1 / Phase 22024-12-03