Trials / Recruiting
RecruitingNCT06036693
MPS (RaDiCo Cohort) (RaDiCo-MPS)
Mucopolysaccharidosis Patients in France in the Era of Specific Therapeutics
- Status
- Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 1,000 (estimated)
- Sponsor
- Institut National de la Santé Et de la Recherche Médicale, France · Other Government
- Sex
- All
- Age
- —
- Healthy volunteers
- Not accepted
Summary
The goal of this observational study is to characterize the epidemiology and natural history of MPS diseases by building a retrospective and prospective collection of extensive phenotypic data from French MPS patients.
Conditions
- Mucopolysaccharidosis I
- Mucopolysaccharidosis II
- Mucopolysaccharidosis III
- Mucopolysaccharidosis IV
- Mucopolysaccharidosis VI
- Mucopolysaccharidosis VII
- Mucopolysaccharidosis IX
- Multiple Sulfatase Deficiency Disease
Timeline
- Start date
- 2017-12-20
- Primary completion
- 2026-12-01
- Completion
- 2026-12-01
- First posted
- 2023-09-14
- Last updated
- 2026-02-11
Locations
23 sites across 1 country: France
Source: ClinicalTrials.gov record NCT06036693. Inclusion in this directory is not an endorsement.