Trials / Conditions / Mucopolysaccharidosis III
Mucopolysaccharidosis III
5 registered clinical trials studyying Mucopolysaccharidosis III — 3 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Study of Cannabidiol in Sanfilippo Syndrome NCT06333041 | Lundquist Institute for Biomedical Innovation at Harbor-UCLA Medical Center | Phase 2 / Phase 3 |
| Completed | Open-label Study of Anakinra in MPS III NCT04018755 | Lynda E Polgreen | Phase 1 / Phase 2 |
| Terminated | Gene Transfer Study of ABO-102 in Patients With Middle and Advanced Phases of MPS IIIA Disease NCT04088734 | Ultragenyx Pharmaceutical Inc | Phase 1 / Phase 2 |
| Recruiting | MPS (RaDiCo Cohort) (RaDiCo-MPS) NCT06036693 | Institut National de la Santé Et de la Recherche Médicale, France | — |
| Recruiting | Phase I/II/III Gene Transfer Clinical Trial of scAAV9.U1a.hSGSH NCT02716246 | Ultragenyx Pharmaceutical Inc | Phase 2 / Phase 3 |