Clinical Trials Directory

Trials / Conditions / Mucopolysaccharidosis VII

Mucopolysaccharidosis VII

8 registered clinical trials studyying Mucopolysaccharidosis VII — 4 currently recruiting.

StatusTrialSponsorPhase
CompletedBaby Detect : Genomic Newborn Screening
NCT05687474
Centre Hospitalier Universitaire de Liege—
RecruitingRegistry of Patients Diagnosed With Lysosomal Storage Diseases
NCT05619900
University of California, San Francisco—
Enrolling By InvitationScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
NCT05368038
Albert Einstein College of Medicine—
RecruitingMucopolysaccharidosis VII Disease Monitoring Program
NCT03604835
Ultragenyx Pharmaceutical Inc—
RecruitingMPS (RaDiCo Cohort) (RaDiCo-MPS)
NCT06036693
Institut National de la Santé Et de la Recherche Médicale, France—
CompletedA Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Muco
NCT02432144
Ultragenyx Pharmaceutical IncPhase 3
CompletedStudy of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharido
NCT02418455
Ultragenyx Pharmaceutical IncPhase 2
AvailableExpanded Access to Mepsevii
NCT03775174
Ultragenyx Pharmaceutical Inc—