Trials / Available

AvailableNCT03775174

Expanded Access to Mepsevii

Status: Available
Phase: —
Study type: Expanded Access
Enrollment: —

Sponsor: Ultragenyx Pharmaceutical Inc · Industry
Sex: All
Age: —
Healthy volunteers: —

Summary

Individual patient expanded access requests may be considered for patients who have no other treatment options

Detailed description

Expanded access may be available outside of the US in countries prior to approval by the local regulatory agencies. For full details, please visit the links provided below.

Conditions

MPS VII
Mucopolysaccharidosis VII
Sly Syndrome

Interventions

Type	Name	Description
DRUG	Mepsevii

Timeline

First posted: 2018-12-13
Last updated: 2026-04-07

Source: ClinicalTrials.gov record NCT03775174. Inclusion in this directory is not an endorsement.