Clinical Trials Directory

Trials / Conditions / Sly Syndrome

Sly Syndrome

8 registered clinical trials studyying Sly Syndrome — 1 currently recruiting.

StatusTrialSponsorPhase
RecruitingMucopolysaccharidosis VII Disease Monitoring Program
NCT03604835
Ultragenyx Pharmaceutical Inc—
CompletedA Study of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Therapy in Subjects With Muco
NCT02432144
Ultragenyx Pharmaceutical IncPhase 3
CompletedStudy of UX003 Recombinant Human Beta-Glucuronidase (rhGUS) Enzyme Replacement Treatment in Mucopolysaccharido
NCT02418455
Ultragenyx Pharmaceutical IncPhase 2
CompletedA Phase 3 Study of UX003 Recombinant Human Betaglucuronidase (rhGUS) Enzyme Replacement Therapy in Patients Wi
NCT02230566
Ultragenyx Pharmaceutical IncPhase 3
Active Not RecruitingMT2013-31: Allo HCT for Metabolic Disorders and Severe Osteopetrosis
NCT02171104
Masonic Cancer Center, University of MinnesotaPhase 2
CompletedAllogeneic Bone Marrow Transplant for Inherited Metabolic Disorders
NCT01043640
Masonic Cancer Center, University of MinnesotaPhase 2
TerminatedHematopoietic Stem Cell Transplantation (HCT) for Inborn Errors of Metabolism
NCT00668564
Masonic Cancer Center, University of MinnesotaPhase 2
AvailableExpanded Access to Mepsevii
NCT03775174
Ultragenyx Pharmaceutical Inc—