Clinical Trials Directory

Trials / Completed

CompletedNCT02795767

A Study of Emicizumab Administered Subcutaneously (SC) in Pediatric Participants With Hemophilia A and Factor VIII (FVIII) Inhibitors

A Multicenter, Open-Label, Phase III Clinical Trial to Evaluate the Efficacy, Safety, and Pharmacokinetics of Subcutaneous Administration of Emicizumab in Hemophilia A Pediatric Patients With Inhibitors

Status
Completed
Phase
Phase 3
Study type
Interventional
Enrollment
88 (actual)
Sponsor
Hoffmann-La Roche · Industry
Sex
All
Age
17 Years
Healthy volunteers
Not accepted

Summary

This non-randomized, multicenter, open-label, Phase III clinical study will evaluate the efficacy, safety, and pharmacokinetics of emicizumab administered subcutaneously initially once weekly (QW) in pediatric participants with hemophilia A with FVIII inhibitors. This study will open two additional non-randomized cohorts to investigate once every 2 weeks (Q2W) and once every 4 weeks (Q4W) regimens in pediatric participants.

Conditions

Interventions

TypeNameDescription
DRUGEmicizumabEmicizumab will be administered as per the schedule specified in the respective arm.

Timeline

Start date
2016-07-22
Primary completion
2018-04-30
Completion
2020-11-11
First posted
2016-06-10
Last updated
2021-06-02
Results posted
2019-04-10

Locations

28 sites across 10 countries: United States, Costa Rica, France, Germany, Italy, Japan, South Africa, Spain, Turkey (Türkiye), United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT02795767. Inclusion in this directory is not an endorsement.