Trials / Completed
CompletedNCT02704273
A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects
INCEPTUS: A Prospective, Non-Interventional Clinical Assessment Study in X Linked Myotubular Myopathy (XLMTM) Subjects Aged 3 Years and Younger
- Status
- Completed
- Phase
- —
- Study type
- Observational
- Enrollment
- 34 (actual)
- Sponsor
- Astellas Gene Therapies · Industry
- Sex
- Male
- Age
- 3 Years
- Healthy volunteers
- Not accepted
Summary
This is a pre-Phase 1 prospective, non interventional clinical assessment study to evaluate XLMTM subjects aged 3 years and younger. Many of these clinically relevant measures have not yet been routinely assessed in this population and may provide important insight on the natural history of XLMTM and for future evaluation of potential therapies.
Conditions
Timeline
- Start date
- 2016-07-01
- Primary completion
- 2019-09-01
- Completion
- 2019-09-01
- First posted
- 2016-03-10
- Last updated
- 2022-07-29
Locations
8 sites across 5 countries: United States, Canada, France, Germany, United Kingdom
Source: ClinicalTrials.gov record NCT02704273. Inclusion in this directory is not an endorsement.