Trials / Conditions / X-linked Myotubular Myopathy
X-linked Myotubular Myopathy
8 registered clinical trials studyying X-linked Myotubular Myopathy — 3 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Study of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators NCT07052929 | Astellas Gene Therapies | Phase 1 / Phase 2 |
| Recruiting | A Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition NCT06581146 | Astellas Gene Therapies | — |
| Terminated | Tamoxifen Therapy for Myotubular Myopathy NCT04915846 | James Dowling | Phase 1 / Phase 2 |
| Active Not Recruiting | A Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM) NCT03199469 | Astellas Gene Therapies | Phase 2 / Phase 3 |
| Completed | A Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects NCT02704273 | Astellas Gene Therapies | — |
| Completed | Respiratory Muscle Function in Untreated X-Linked Myotubular Myopathy (XLMTM) NCT02453152 | University of Florida | — |
| Completed | Myotubular Myopathy Event Study NCT01840657 | Cure CMD | — |
| Recruiting | Myotubular and Centronuclear Myopathy Patient Registry NCT04064307 | Newcastle-upon-Tyne Hospitals NHS Trust | — |