Clinical Trials Directory

Trials / Sponsors / Astellas Gene Therapies

Astellas Gene Therapies

Industry · 8 registered clinical trials — 2 currently recruiting.

StatusTrialPhaseStarted
RecruitingStudy of ASP2957 in Male Participants With X-linked Myotubular Myopathy Who Need Ventilators
X-Linked Myotubular Myopathy
Phase 1 / Phase 22025-12-15
RecruitingA Study to Check Liver Health in Boys With XLMTM, a Serious Genetic Muscle Condition
X-Linked Myotubular Myopathy
—2025-05-19
WithdrawnA Study of ASP2016 in Adults Who Have Heart Disease Associated With Friedreich Ataxia
Friedreich Ataxia, Cardiomyopathy
Phase 12024-11-08
Active Not RecruitingA Study About Antibody Levels and Biomarkers in the Blood in People With Late-onset Pompe Disease
Pompe Disease (Late-onset)
N/A2024-02-01
Active Not RecruitingGene Transfer Study in Patients With Late Onset Pompe Disease
Pompe Disease (Late-onset)
Phase 1 / Phase 22020-10-27
Active Not RecruitingA Study of AT132 in Young Children With X-Linked Myotubular Myopathy (XLMTM)
X-Linked Myotubular Myopathy
Phase 2 / Phase 32017-08-02
CompletedA Clinical Assessment Study in X-Linked Myotubular Myopathy (XLMTM) Subjects
X-linked Myotubular Myopathy
—2016-07-01
CompletedA Medical Chart Review of Patients With X-Linked Myotubular Myopathy (XLMTM)
Males With X-linked Myotubular Myopathy (XLMTM)
—2014-09-01