Trials / Conditions / Niemann-Pick Type C Disease
Niemann-Pick Type C Disease
5 registered clinical trials studyying Niemann-Pick Type C Disease — 3 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or NCT07399704 | Azafaros A.G. | Phase 2 |
| Recruiting | A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For NCT07082725 | Azafaros A.G. | Phase 3 |
| Recruiting | A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For NCT07054515 | Azafaros A.G. | Phase 3 |
| Terminated | Niemann-Pick Type C Treatment With Adrabetadex for Symptoms of Brain and Nervous System NCT03643562 | Mandos LLC | Phase 3 |
| Completed | Miglustat in Niemann-Pick Type C Disease NCT00517153 | Actelion | Phase 2 |