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Azafaros A.G.
Industry · 6 registered clinical trials —
4 currently recruiting
.
Status
Trial
Phase
Started
Recruiting
A Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or
GM2 Gangliosidosis, Niemann-Pick Type C Disease
Phase 2
2026-02-04
Recruiting
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
Gangliosidoses, GM2, Gangliosidosis, GM1
Phase 3
2025-06-30
Recruiting
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
Niemann-Pick Type C Disease, GM1 Gangliosidosis, GM2 Gangliosidosis
Phase 3
2025-06-30
Recruiting
A Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
Niemann-Pick Type C Disease
Phase 3
2025-06-30
Active Not Recruiting
Phase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Pa
GM2 Gangliosidosis, Niemann-Pick Disease, Type C
Phase 2
2023-04-24
Completed
GM1 and GM2 Gangliosidosis PROspective Neurological Disease TrajectOry Study (PRONTO)
GM1 Gangliosidosis, Sandhoff Disease, Tay-Sachs Disease
—
2022-02-22