Clinical Trials Directory

Trials / Sponsors / Azafaros A.G.

Azafaros A.G.

Industry · 6 registered clinical trials4 currently recruiting.

StatusTrialPhaseStarted
RecruitingA Study to Evaluate the Safety and Efficacy of Nizubaglustat (AZ-3102) in Patients With GM2 Gangliosidosis or
GM2 Gangliosidosis, Niemann-Pick Type C Disease
Phase 22026-02-04
RecruitingA Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
Gangliosidoses, GM2, Gangliosidosis, GM1
Phase 32025-06-30
RecruitingA Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
Niemann-Pick Type C Disease, GM1 Gangliosidosis, GM2 Gangliosidosis
Phase 32025-06-30
RecruitingA Study to Evaluate the Safety and Efficacy of Oral Nizubaglustat (AZ-3102) in Late-infantile and Juvenile For
Niemann-Pick Type C Disease
Phase 32025-06-30
Active Not RecruitingPhase 2 Study Evaluating the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of Oral AZ-3102 in Pa
GM2 Gangliosidosis, Niemann-Pick Disease, Type C
Phase 22023-04-24
CompletedGM1 and GM2 Gangliosidosis PROspective Neurological Disease TrajectOry Study (PRONTO)
GM1 Gangliosidosis, Sandhoff Disease, Tay-Sachs Disease
2022-02-22