Clinical Trials Directory

Trials / Conditions / Niemann-Pick Disease

Niemann-Pick Disease

10 registered clinical trials studyying Niemann-Pick Disease — 1 currently recruiting.

StatusTrialSponsorPhase
Not Yet RecruitingNational Multicentre Study of the Natural History of Acid Sphingo-myelinase Deficiency in Adults and Children
NCT06985212
Wladimir MAUHIN, Dr—
WithdrawnBiomarker for Niemann Pick Type C Disease (BioNPC)
NCT01306604
CENTOGENE GmbH Rostock—
UnknownInvestigating Lysosomal Storage Diseases in Minority Groups
NCT02120235
O & O Alpan LLC—
CompletedHuman Placental-Derived Stem Cell Transplantation
NCT01586455
New York Medical CollegePhase 1
TerminatedPhase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders
NCT01372228
Talaris Therapeutics Inc.Phase 1 / Phase 2
CompletedUnrelated Hematopoietic Stem Cell Transplantation(HSCT) for Genetic Diseases of Blood Cells
NCT00730314
Children's Hospital Los AngelesPhase 1 / Phase 2
TerminatedSafety Study of rhASM Enzyme Replacement Therapy in Adults With Acid Sphingomyelinase Deficiency (Niemann-Pick
NCT00410566
Genzyme, a Sanofi CompanyPhase 1
UnknownStudy of Pulmonary Complications in Pediatric Patients With Storage Disorders Undergoing Allogeneic Hematopoie
NCT00005900
Fairview University Medical Center—
CompletedStem Cell Transplant for Inborn Errors of Metabolism
NCT00176904
Masonic Cancer Center, University of MinnesotaPhase 2 / Phase 3
CompletedPET Scan of Brain Metabolism in Relation to Age and Disease
NCT00001972
National Institute of Neurological Disorders and Stroke (NINDS)—