Trials / Conditions / Metachromatic Leukodystrophy (MLD)

Metachromatic Leukodystrophy (MLD)

11 registered clinical trials studyying Metachromatic Leukodystrophy (MLD) — 3 currently recruiting.

Status	Trial	Sponsor	Phase
Recruiting	Lentiviral Hematopoietic Stem Cell Gene Therapy for MLD NCT07046338	Shenzhen Geno-Immune Medical Institute	N/A
Recruiting	Direct Lentiviral Injection Gene Therapy for MLD NCT03725670	Shenzhen Geno-Immune Medical Institute	N/A
Withdrawn	A Study to Learn About Metachromatic Leukodystrophy (MLD) in Children in Spain NCT05755568	Takeda	—
Active Not Recruiting	A Study of Intrathecal SHP611 in Children With Metachromatic Leukodystrophy NCT03771898	Shire	Phase 2
Terminated	Natural History Study of Children With Metachromatic Leukodystrophy NCT01963650	Shire	—
Active Not Recruiting	An Efficacy and Safety Study of HGT-1110 in Participants With Metachromatic Leukodystrophy NCT01887938	Shire	Phase 1 / Phase 2
Completed	Multicenter Study of HGT-1110 Administered Intrathecally in Children With Metachromatic Leukodystrophy (MLD) NCT01510028	Shire	Phase 1 / Phase 2
Terminated	Phase I/II Pilot Study of Mixed Chimerism to Treat Inherited Metabolic Disorders NCT01372228	Talaris Therapeutics Inc.	Phase 1 / Phase 2
Recruiting	Rare Disease Patient Registry & Natural History Study - Coordination of Rare Diseases at Sanford NCT01793168	Sanford Health	—
Completed	Allogeneic Bone Marrow Transplant for Inherited Metabolic Disorders NCT01043640	Masonic Cancer Center, University of Minnesota	Phase 2
Completed	Metazym for the Treatment of Patients With Late Infantile Metachromatic Leukodystrophy (MLD) NCT00418561	Shire	Phase 1