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Active Not RecruitingNCT07274826

Diagnostic Creteria of Acid Sphingomyelinase Deficiency (ASMD)

Intact Potential Symptoms and Biomarker Analysis in Diagnosis of Acid Sphingomyelinase Deficiency (ASMD)

Status
Active Not Recruiting
Phase
Study type
Observational
Enrollment
7 (estimated)
Sponsor
Sohag University · Academic / Other
Sex
All
Age
Healthy volunteers
Not accepted

Summary

Acid sphingomyelinase Deficiency known as Neiman \_PICK disease is a group of rare genetic diseases. This study includes analysis of clinical manifestations in patients with ASMD and investigations done for diagnosis of these patients

Conditions

Timeline

Start date
2025-11-20
Primary completion
2026-08-10
Completion
2026-09-10
First posted
2025-12-10
Last updated
2025-12-10

Locations

1 site across 1 country: Egypt

Source: ClinicalTrials.gov record NCT07274826. Inclusion in this directory is not an endorsement.

Diagnostic Creteria of Acid Sphingomyelinase Deficiency (ASMD) (NCT07274826) · Clinical Trials Directory