Trials / Conditions / Acid Sphingomyelinase Deficiency (ASMD)
Acid Sphingomyelinase Deficiency (ASMD)
3 registered clinical trials studyying Acid Sphingomyelinase Deficiency (ASMD) — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Active Not Recruiting | Diagnostic Creteria of Acid Sphingomyelinase Deficiency (ASMD) NCT07274826 | Sohag University | — |
| Not Yet Recruiting | National Multicentre Study of the Natural History of Acid Sphingo-myelinase Deficiency in Adults and Children NCT06985212 | Wladimir MAUHIN, Dr | — |
| Completed | Data Analysis of Adult and Pediatric Participants With Acid Sphingomyelinase Deficiency (ASMD) on Early Access NCT05359276 | Sanofi | — |