Trials / Recruiting
RecruitingNCT06712810
Q702 for the Treatment of Patients With Hematologic Malignancies
MC220806: Phase I Study Evaluating the Efficacy of CSF1R and TAM Receptor or Inhibition in Hematologic Malignancies With Q702, a Small Molecular Inhibitor
- Status
- Recruiting
- Phase
- Phase 1
- Study type
- Interventional
- Enrollment
- 46 (estimated)
- Sponsor
- Mayo Clinic · Academic / Other
- Sex
- All
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
This phase I trial tests the safety, side effects, and best dose of Q702 in treating patients with hematologic malignancies. Q702 is in a class of medications called immunomodulatory agents. It works by helping the immune system kill cancer cells and by helping the bone marrow to produce normal blood cells. Giving Q702 may be safe, tolerable and/or effective in treating patients with hematologic malignancies.
Detailed description
PRIMARY OBJECTIVES: I. Establish the highest dose of Q702 tested that has acceptable tolerability and safety. (Dose determination) II. Safety and overall response assessment in patients with hematologic malignancies who have been treated with Q702. (Dose expansion) SECONDARY OBJECTIVES: I. Assessment of progression-free survival and overall survival. II. Safety and tolerability of Q702. EXPLORATORY OBJECTIVE: I. Improvement of quality of life (QOL) assessed by using the Patient-Reported Outcomes Measurement Information System (PROMIS) tool compared to pretreatment values. CORRELATIVE OBJECTIVES: I. Programmed Death-Ligand 1 (PD-L1), Colony stimulating factor 1 receptor (CSF1R) expression of tumor before and after treatment. II. M2 macrophage population assessed through flow cytometry by using peripheral blood before and after treatment. III. Serum cytokine interferon gamma, Interleukin (IL)-1b, IL-6, IL-4, IL-10, IL-13, C-reactive protein (CRP) and erythrocyte sedimentation rate (ESR) before and after each cycle of therapy. IV. Assessment of inflammatory markers before and after treatment with Q702. V. Assessment of cluster of differentiation 4 (CD4)/cluster of differentiation 8 (CD8) infiltration in the tumor involvement before, during, and after treatment with Q702. OUTLINE: This is a dose-escalation study of Q702 followed by a dose-expansion study. Patients receive Q702 orally (PO) daily (QD) on days 1-7 and 15-21 of each cycle. Cycles repeat every 28 days in the absence of disease progression or unacceptable toxicity. After 6 cycles, patients who have not progressed/relapsed may continue on therapy at their current dose at medical doctor (MD)/patient discretion for an additional 6 cycles. Patients undergo blood and urine sample collection and may undergo positron emission tomography (PET) scan/computed tomography (CT) scan or magnetic resonance imaging (MRI) and bone marrow aspiration and biopsy throughout the study. After completion of study treatment, patients are followed up every 6 months and at progressive disease for 2 years.
Conditions
- Hematopoietic and Lymphatic System Neoplasm
- Histiocytic Sarcoma
- Malignant Histiocytosis
- Peripheral T-Cell Lymphoma, Not Otherwise Specified
- Primary Cutaneous T-Cell Non-Hodgkin Lymphoma
- Recurrent Chronic Lymphocytic Leukemia
- Recurrent Chronic Myelomonocytic Leukemia
- Recurrent Follicular Lymphoma
- Recurrent Langerhans Cell Histiocytosis
- Recurrent Lymphoplasmacytic Lymphoma
- Recurrent Myelodysplastic Syndrome
- Recurrent Myelofibrosis
- Recurrent Small Lymphocytic Lymphoma
- Recurrent Waldenstrom Macroglobulinemia
- Refractory Chronic Lymphocytic Leukemia
- Refractory Chronic Myelomonocytic Leukemia
- Refractory Erdheim-Chester Disease
- Refractory Follicular Lymphoma
- Refractory Langerhans Cell Histiocytosis
- Refractory Lymphoplasmacytic Lymphoma
- Refractory Myelodysplastic Syndrome
- Refractory Myelofibrosis
- Refractory Small Lymphocytic Lymphoma
- Refractory Waldenstrom Macroglobulinemia
- Rosai-Dorfman-Destombes Disease
- Primary Central Nervous System Lymphoma
- Recurrent Blastic Plasmacytoid Dendritic Cell Neoplasm
- Recurrent Erdheim-Chester Disease
- Recurrent Fibroblastic Reticular Cell Sarcoma
- Recurrent Histiocytic Sarcoma
- Recurrent Interdigitating Dendritic Cell Sarcoma
- Recurrent Rosai-Dorfman-Destombes Disease
- Refractory Blastic Plasmacytoid Dendritic Cell Neoplasm
- Refractory Fibroblastic Reticular Cell Sarcoma
- Refractory Histiocytic Sarcoma
- Refractory Interdigitating Dendritic Cell Sarcoma
- Refractory Rosai-Dorfman-Destombes Disease
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | Axl/Mer/CSF1R Inhibitor Q702 | Given PO |
| PROCEDURE | Biospecimen Collection | Undergo blood and urine sample collection |
| PROCEDURE | Bone Marrow Aspiration | Undergo bone marrow biopsy and aspiration |
| PROCEDURE | Bone Marrow Biopsy | Undergo bone marrow biopsy and aspiration |
| PROCEDURE | Computed Tomography | Undergo CT scan |
| PROCEDURE | Magnetic Resonance Imaging | Undergo MRI |
| PROCEDURE | Positron Emission Tomography | Undergo PET scan |
| OTHER | Survey Administration | Ancillary study |
Timeline
- Start date
- 2025-08-27
- Primary completion
- 2030-09-15
- Completion
- 2030-09-15
- First posted
- 2024-12-02
- Last updated
- 2025-10-10
Locations
2 sites across 1 country: United States
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT06712810. Inclusion in this directory is not an endorsement.