Trials / Recruiting
RecruitingNCT06488924
An Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
- Status
- Recruiting
- Phase
- Phase 1 / Phase 2
- Study type
- Interventional
- Enrollment
- 10 (estimated)
- Sponsor
- JCR Pharmaceuticals Co., Ltd. · Industry
- Sex
- All
- Age
- 17 Years
- Healthy volunteers
- Not accepted
Summary
A Phase I/ II, open-label study, designed to evaluate the safety and explore efficacy of the study drug in development for the treatment of MPS IIIB patients.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | JR-446 | IV infusion |
Timeline
- Start date
- 2024-11-05
- Primary completion
- 2030-04-30
- Completion
- 2030-04-30
- First posted
- 2024-07-05
- Last updated
- 2025-09-02
Locations
3 sites across 1 country: Japan
Source: ClinicalTrials.gov record NCT06488924. Inclusion in this directory is not an endorsement.