Clinical Trials Directory

Trials / Conditions / Mucopolysaccharidosis III-B

Mucopolysaccharidosis III-B

3 registered clinical trials studyying Mucopolysaccharidosis III-B2 currently recruiting.

StatusTrialSponsorPhase
RecruitingAn Open-label Phase I/II Study of JR-446 in Mucopolysaccharidosis Type IIIB
NCT06488924
JCR Pharmaceuticals Co., Ltd.Phase 1 / Phase 2
Enrolling By InvitationScreenPlus: A Comprehensive, Flexible, Multi-disorder Newborn Screening Program
NCT05368038
Albert Einstein College of Medicine
TerminatedA Long-term Follow-up Study of Patients With MPS IIIB Treated With ABO-101
NCT04655911
Abeona Therapeutics, Inc