Clinical Trials Directory

Trials / Recruiting

RecruitingNCT06271512

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel

A Safety and Effectiveness Registry Study of Patients with Β-Thalassemia Treated with Betibeglogene Autotemcel (the Glostar Registry)

Status
Recruiting
Phase
Study type
Observational
Enrollment
150 (estimated)
Sponsor
Genetix Biotherapeutics Inc. · Industry
Sex
All
Age
Healthy volunteers
Not accepted

Summary

The main aim of this study is to collect real-world longitudinal data on participants with β-thalassemia treated with betibeglogene autotemcel (beti-cel) in the post marketing setting. To assess the long-term safety, including the risk of newly diagnosed malignancies, after treatment with beti-cel and evaluate the long-term effectiveness of treatment with beti-cel.

Conditions

Interventions

TypeNameDescription
OTHERNo InterventionThis is non-interventional study.

Timeline

Start date
2024-01-23
Primary completion
2043-12-01
Completion
2043-12-01
First posted
2024-02-21
Last updated
2025-02-11

Locations

6 sites across 1 country: United States

Source: ClinicalTrials.gov record NCT06271512. Inclusion in this directory is not an endorsement.

A Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel (NCT06271512) · Clinical Trials Directory