Clinical Trials Directory

Trials / Sponsors / Genetix Biotherapeutics Inc.

Genetix Biotherapeutics Inc.

Industry · 14 registered clinical trials — 3 currently recruiting.

StatusTrialPhaseStarted
RecruitingA Study of Participants With Cerebral Adrenoleukodystrophy (CALD) Treated With Elivaldogene Autotemcel
Cerebral Adrenoleukodystrophy (CALD)
—2024-03-27
RecruitingA Study of Participants with Β-Thalassemia Treated with Betibeglogene Autotemcel
Beta-Thalassemia
—2024-01-23
Enrolling By InvitationLong-term Follow-up of Subjects with Sickle Cell Disease Treated with Ex Vivo Gene Therapy
Sickle Cell Disease
—2020-10-21
Active Not RecruitingA Study Evaluating Gene Therapy With BB305 Lentiviral Vector in Sickle Cell Disease
Sickle Cell Disease
Phase 32020-02-14
CompletedA Clinical Study to Assess the Efficacy and Safety of Gene Therapy for the Treatment of Cerebral Adrenoleukody
Cerebral Adrenoleukodystrophy (CALD)
Phase 32019-01-24
CompletedA Study Evaluating the Efficacy and Safety of the LentiGlobin® BB305 Drug Product in Participants With Transfu
Beta-Thalassemia
Phase 32017-06-08
CompletedA Study Evaluating the Efficacy and Safety of the LentiGlobin® BB305 Drug Product in Participants With Transfu
Beta-Thalassemia
Phase 32016-08-08
Active Not RecruitingLong-term Follow-up of Participants With Cerebral Adrenoleukodystrophy Who Were Treated With Lenti-D Drug Prod
Cerebral Adrenoleukodystrophy (CALD), Adrenoleukodystrophy (ALD), X-Linked Adrenoleukodystrophy (X-ALD)
—2016-01-22
TerminatedObservational Study to Evaluate Allogeneic HSCT Outcomes for Cerebral Adrenoleukodystrophy (CALD)
X-Linked Adrenoleukodystrophy (X-ALD), Cerebral Adrenoleukodystrophy (CALD), Adrenoleukodystrophy (ALD)
—2015-04-01
CompletedA Study Evaluating the Safety and Efficacy of Lovo-cel in Severe Sickle Cell Disease
Sickle Cell Disease
Phase 1 / Phase 22015-02-02
Active Not RecruitingLong-term Follow-up of Subjects With Transfusion-Dependent β-Thalassemia (TDT) Treated With Ex Vivo Gene Thera
Transfusion-dependent Beta-Thalassemia
—2014-01-01
CompletedA Study of the Efficacy and Safety of Hematopoietic Stem Cells Transduced With Lenti-D Lentiviral Vector for t
Cerebral Adrenoleukodystrophy (CALD)
Phase 2 / Phase 32013-08-21
CompletedA Study Evaluating the Safety and Efficacy of the LentiGlobin BB305 Drug Product in β-Thalassemia Major Partic
β-thalassemia Major
Phase 1 / Phase 22013-08-01
CompletedA Study Evaluating the Safety and Efficacy of LentiGlobin BB305 Drug Product in β-Thalassemia Major (Also Refe
Beta-Thalassemia Major, Sickle Cell Disease
Phase 1 / Phase 22013-06-07