Trials / Recruiting
RecruitingNCT05769621
A Retrospective Study to Characterize Participants With Propionic Acidemia
A Retrospective Cohort Study to Characterize Propionic Acidemia Patients
- Status
- Recruiting
- Phase
- —
- Study type
- Observational
- Enrollment
- 60 (estimated)
- Sponsor
- ModernaTX, Inc. · Industry
- Sex
- All
- Age
- 2 Years
- Healthy volunteers
- Not accepted
Summary
This is a non-interventional, observational, global, multicenter, study describing participant characteristics, clinical outcomes, and event rates in participants with propionic acidemia (PA).
Detailed description
Data will be abstracted through medical record review ensuring inclusion only of data from participants meeting all the inclusion criteria and none of the censoring criteria. Data will be collected retrospectively from study sites, including medical clinics, hospitals and academic medical centers.
Conditions
Timeline
- Start date
- 2023-06-16
- Primary completion
- 2026-09-30
- Completion
- 2026-09-30
- First posted
- 2023-03-15
- Last updated
- 2026-02-05
Locations
29 sites across 9 countries: United States, Australia, Canada, France, Italy, Japan, Netherlands, Spain, United Kingdom
Source: ClinicalTrials.gov record NCT05769621. Inclusion in this directory is not an endorsement.