Trials / Completed
CompletedNCT04995315
Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008
Pyruvate Kinase Deficiency Global Longitudinal Registry Substudy of Protocol AG348-C-008: Cognition in Participants With Pyruvate Kinase Deficiency
- Status
- Completed
- Phase
- —
- Study type
- Observational
- Enrollment
- 13 (actual)
- Sponsor
- Agios Pharmaceuticals, Inc. · Industry
- Sex
- All
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
This is a substudy of Study AG348-C-008, an observational, longitudinal, multicenter, global registry that aims to better understand the longitudinal clinical implications of pyruvate kinase deficiency (PK deficiency). The primary purpose of this study is to describe the cognition of participants with PK deficiency, as objectively measured by the Cogstate Brief Battery (CBB).
Conditions
Timeline
- Start date
- 2021-07-02
- Primary completion
- 2023-09-22
- Completion
- 2023-09-22
- First posted
- 2021-08-06
- Last updated
- 2023-10-16
Locations
3 sites across 3 countries: United States, Italy, Netherlands
Source: ClinicalTrials.gov record NCT04995315. Inclusion in this directory is not an endorsement.