Trials / Terminated
TerminatedNCT04988867
An Open-Label Study of Trofinetide for the Treatment of Girls Two to Five Years of Age Who Have Rett Syndrome
- Status
- Terminated
- Phase
- Phase 2 / Phase 3
- Study type
- Interventional
- Enrollment
- 15 (actual)
- Sponsor
- ACADIA Pharmaceuticals Inc. · Industry
- Sex
- Female
- Age
- 2 Years – 5 Years
- Healthy volunteers
- Not accepted
Summary
To investigate the safety and tolerability of long-term treatment with oral trofinetide in girls with Rett syndrome
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | Trofinetide | Trofinetide solution of 10-30 mL based on subject's weight at Baseline, administered twice daily by mouth or gastrostomy tube (G-tube) |
Timeline
- Start date
- 2021-09-22
- Primary completion
- 2023-05-31
- Completion
- 2023-05-31
- First posted
- 2021-08-04
- Last updated
- 2024-09-24
- Results posted
- 2024-09-24
Locations
7 sites across 1 country: United States
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT04988867. Inclusion in this directory is not an endorsement.