Clinical Trials Directory

Trials / Completed

CompletedNCT04537793

Evaluation of ELX/TEZ/IVA in Cystic Fibrosis (CF) Subjects 2 Through 5 Years

A Phase 3 Study Evaluating the Safety, Tolerability, and Pharmacokinetics of Elexacaftor/Tezacaftor/Ivacaftor Triple Combination Therapy in Cystic Fibrosis Subjects 2 Through 5 Years of Age

Status
Completed
Phase
Phase 3
Study type
Interventional
Enrollment
83 (actual)
Sponsor
Vertex Pharmaceuticals Incorporated · Industry
Sex
All
Age
2 Years – 5 Years
Healthy volunteers
Not accepted

Summary

This study will evaluate the safety, tolerability, pharmacokinetics, pharmacodynamics and efficacy of elexacaftor (ELX)/tezacaftor (TEZ)/ivacaftor (IVA) triple combination therapy in CF subjects 2 through 5 years of age.

Conditions

Interventions

TypeNameDescription
DRUGELX/TEZ/IVAFixed dose combination granules for oral administration.
DRUGIVAGranules for oral administration.

Timeline

Start date
2020-11-19
Primary completion
2022-06-03
Completion
2022-06-03
First posted
2020-09-03
Last updated
2023-06-28
Results posted
2023-06-28

Locations

22 sites across 5 countries: United States, Australia, Canada, Germany, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT04537793. Inclusion in this directory is not an endorsement.