Trials / Withdrawn
WithdrawnNCT04480476
A Retrospective, Natural History Study in Children With CLN2
A Retrospective, Chart Review Study to Evaluate Ocular Disease Progression in Children With Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2)
- Status
- Withdrawn
- Phase
- —
- Study type
- Observational
- Enrollment
- 0 (actual)
- Sponsor
- REGENXBIO Inc. · Industry
- Sex
- All
- Age
- —
- Healthy volunteers
- Not accepted
Summary
This is a multi center, retrospective, chart review study to document the evolution of ocular disease progression in pediatric patients with CLN2.
Detailed description
CLN2 is a rare disease with limited available ocular natural history data. While current standard of care slows motor degeneration, it is not known to treat the ocular manifestations of disease. This study is planned to document, through retrospective data collection, ocular disease progression in children with a clinical presentation consistent with CLN2. No investigational product is administered in this retrospective, chart review study.
Conditions
Timeline
- Start date
- 2021-03-31
- Primary completion
- 2022-04-01
- Completion
- 2022-04-01
- First posted
- 2020-07-21
- Last updated
- 2021-11-01
Source: ClinicalTrials.gov record NCT04480476. Inclusion in this directory is not an endorsement.