Trials / Sponsors / REGENXBIO Inc.
REGENXBIO Inc.
Industry · 17 registered clinical trials — 4 currently recruiting.
| Status | Trial | Phase | Started |
|---|---|---|---|
| Suspended | RGX-121-3102 Gene Therapy in Participants With MPS II (Hunter Syndrome) MPS II, Hunter Syndrome (MPS II) | Phase 3 | 2025-11-25 |
| Enrolling By Invitation | Long Term Follow-up for RGX-202 Duchenne Muscular Dystrophy | — | 2024-05-08 |
| Enrolling By Invitation | Long Term Follow-Up for RGX-111 Mucopolysaccharidosis I | — | 2023-07-24 |
| Recruiting | AFFINITY DUCHENNE: RGX-202 Gene Therapy in Participants With Duchenne Muscular Dystrophy (DMD) Duchenne Muscular Dystrophy | Phase 2 / Phase 3 | 2023-01-04 |
| Recruiting | AFFINITY BEYOND: Anti-AAV8 Antibody Assessment Study of Males With DMD Duchenne Muscular Dystrophy | — | 2022-12-20 |
| Withdrawn | Mucopolysaccharidosis Type II Observational Mucopolysaccharidosis II | — | 2022-03-01 |
| Withdrawn | An Observational Study in Children With CLN2 Batten Disease Neuronal Ceroid Lipofuscinosis Type 2 (CLN2) | — | 2021-03-31 |
| Withdrawn | A Retrospective, Natural History Study in Children With CLN2 Late-infantile Neuronal Ceroid Lipofuscinosis Type 2 (CLN2) | — | 2021-03-31 |
| Unknown | Long-term Follow-Up for RGX-121 Mucopolysaccharidosis II | — | 2021-03-14 |
| Completed | RGX-121 Gene Therapy in Children 5 Years of Age and Over With MPS II (Hunter Syndrome) Mucopolysaccharidosis Type II (MPS II) | Phase 1 / Phase 2 | 2021-03-11 |
| Completed | Identifying and Genotyping Homozygous Familial Hypercholesterolemia (HoFH) Patients Homozygous Familial Hypercholesterolemia (HoFH) | — | 2019-12-04 |
| Unknown | A Long-term Follow-up Study to Evaluate the Safety and Efficacy of RGX-501 Homozygous Familial Hypercholesterolemia (HoFH) | — | 2019-09-30 |
| Suspended | RGX-111 Gene Therapy in Patients With MPS I Mucopolysaccharidosis Type I (MPS I), Hurler Syndrome, Hurler-Scheie Syndrome | Phase 1 / Phase 2 | 2019-04-03 |
| Active Not Recruiting | CAMPSIITE™ RGX-121 Gene Therapy in Subjects With MPS II (Hunter Syndrome) Mucopolysaccharidosis Type II (MPS II) | Phase 2 / Phase 3 | 2018-09-27 |
| Completed | Mucopolysaccharidosis Type II Natural History Mucopolysaccharidosis II | — | 2017-09-27 |
| Completed | Safety and Tolerability of RGX-314 (Investigational Product) Gene Therapy for Neovascular AMD Trial Neovascular Age-related Macular Degeneration, Wet Age-related Macular Degeneration | Phase 1 / Phase 2 | 2017-03-29 |
| Terminated | A Gene Therapy Study for Homozygous Familial Hypercholesterolemia (HoFH) Homozygous Familial Hypercholesterolemia (HoFH) | Phase 1 / Phase 2 | 2016-03-01 |