Clinical Trials Directory

Trials / Completed

CompletedNCT04362761

A Study Evaluating the Long-Term Safety of Elexacaftor Combination Therapy

A Phase 3b Open-label Extension Study Evaluating the Safety of Elexacaftor/Tezacaftor/Ivacaftor Combination Therapy in Cystic Fibrosis Subjects

Status
Completed
Phase
Phase 3
Study type
Interventional
Enrollment
172 (actual)
Sponsor
Vertex Pharmaceuticals Incorporated · Industry
Sex
All
Age
12 Years
Healthy volunteers
Not accepted

Summary

This study evaluate the long-term safety and tolerability of elexacaftor (ELX)/tezacaftor (TEZ)/ ivacaftor (IVA) triple combination (TC) in participants with cystic fibrosis (CF) who are homozygous for F508del.

Conditions

Interventions

TypeNameDescription
DRUGELX/TEZ/IVAFixed-dose combination (FDC) tablet for oral administration.
DRUGIVATablet for oral administration.

Timeline

Start date
2020-05-04
Primary completion
2022-12-21
Completion
2022-12-21
First posted
2020-04-27
Last updated
2023-07-28
Results posted
2023-07-28

Locations

29 sites across 4 countries: Australia, Belgium, Germany, United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT04362761. Inclusion in this directory is not an endorsement.