Trials / Completed
CompletedNCT04072237
Study of Coagulation Faction VIIa Variant Marzeptacog Alfa (Activated) in Adult Subjects With Hemophilia
Phase 1 Study to Evaluate the Pharmacokinetics, Pharmacodynamics, and Safety of Ascending Doses of Subcutaneous Marzeptacog Alfa (Activated) in Adult Subjects With Hemophilia
- Status
- Completed
- Phase
- Phase 1
- Study type
- Interventional
- Enrollment
- 11 (actual)
- Sponsor
- Catalyst Biosciences · Industry
- Sex
- Male
- Age
- 18 Years
- Healthy volunteers
- Not accepted
Summary
This multi-center, open label Phase 1 study will evaluate the pharmacokinetics, pharmacodynamics, and safety of a single IV dose of MarzAA followed by ascending single SC doses of MarzAA in adult subjects with moderate or severe Hemophilia A or B, with or without an inhibitor.
Detailed description
This multi-center, open label Phase 1 study will evaluate the pharmacokinetics, pharmacodynamics, and safety of a single IV dose of MarzAA followed by ascending single SC doses of MarzAA in adult subjects with moderate or severe Hemophilia A or B, with or without an inhibitor. The study will enroll at least 8 adult male subjects with moderate or severe Hemophilia A or B with or without an inhibitor, in each dosing stage. Each subject will receive escalating doses of MarzAA for each stage of the study (except for Stage 5, where subjects receive the same dose as in Stage 4 split between two anatomical sites).
Conditions
- Hemophilia A
- Hemophilia B
- Hemophilia A With Inhibitor
- Hemophilia B With Inhibitor
- Hemophilia A Without Inhibitor
- Hemophilia B Without Inhibitor
Interventions
| Type | Name | Description |
|---|---|---|
| BIOLOGICAL | MarzAA (marzeptacog alfa [activated]) | Single intravenous dose and ascending doses of subcutaneous injection of MarzAA (Coagulation Faction VIIa Variant) |
Timeline
- Start date
- 2019-09-24
- Primary completion
- 2020-04-30
- Completion
- 2020-06-17
- First posted
- 2019-08-28
- Last updated
- 2021-09-13
- Results posted
- 2021-07-16
Locations
5 sites across 2 countries: Bulgaria, Russia
Regulatory
- FDA-regulated drug study
Source: ClinicalTrials.gov record NCT04072237. Inclusion in this directory is not an endorsement.