Clinical Trials Directory

Trials / Approved For Marketing

Approved For MarketingNCT04058210

VX-445/TEZ/IVA Expanded Access Program for Cystic Fibrosis (CF) Patients Heterozygous for F508del Mutation and a Minimal Function Mutation (F/MF Genotypes)

VX-445/TEZ/IVA Triple Combination Expanded Access Program for Patients 12 Years of Age and Older With Cystic Fibrosis Who Are Heterozygous for F508del and a Minimal Function CFTR Mutation

Status
Approved For Marketing
Phase
Study type
Expanded Access
Enrollment
Sponsor
Vertex Pharmaceuticals Incorporated · Industry
Sex
All
Age
12 Years
Healthy volunteers

Summary

The purpose of this program is to provide elexacaftor(ELX, VX-445)/tezacaftor(TEZ)/ivacaftor(IVA) combination therapy to CF patients in critical need who are 12 years of age and older, heterozygous for F508del and a minimal function (MF) mutation in response to unsolicited physician requests.

Conditions

Interventions

TypeNameDescription
DRUGELX/TEZ/IVAFixed-dose combination tablet for oral administration.
DRUGIVA150-mg tablet for oral administration.

Timeline

First posted
2019-08-15
Last updated
2019-11-21

Source: ClinicalTrials.gov record NCT04058210. Inclusion in this directory is not an endorsement.