Clinical Trials Directory

Trials / Completed

CompletedNCT03917212

Energy Metabolism in Branched-chain Organic Acidemias

Non-invasive Measurement of Energy Metabolism in Patients With Primary and Secondary Mitochondrial Diseases

Status
Completed
Phase
Study type
Observational
Enrollment
57 (actual)
Sponsor
German Diabetes Center · Academic / Other
Sex
All
Age
5 Years
Healthy volunteers
Accepted

Summary

Energy metabolism and insulin sensitivity were assessed in a case-control study in patients with branched-chain organic acidemias.

Detailed description

Children and adults with branched-chain organic acidemias and matched healthy humans underwent deep metabolic phenotyping using non-invasive magnetic resonance spectroscopy, oral glucose tolerance tests and measurements of leucocyte respirometry in order to assess changes in energy metabolism and insulin sensitivity.

Conditions

Interventions

TypeNameDescription
OTHERNo interventionNo intervention, observational study with metabolic characterisation

Timeline

Start date
2012-03-01
Primary completion
2017-11-01
Completion
2018-03-01
First posted
2019-04-16
Last updated
2019-04-16

Locations

2 sites across 1 country: Germany

Source: ClinicalTrials.gov record NCT03917212. Inclusion in this directory is not an endorsement.