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Trials / Completed

CompletedNCT03853798

Extension Study of AG-348 in Adult Participants With Pyruvate Kinase Deficiency Previously Enrolled in AG-348-006 or AG348-C-007

An Open-Label, Multicenter, Extension Study of AG-348 in Adult Subjects With Pyruvate Kinase Deficiency Previously Enrolled in AG-348 Studies

Status
Completed
Phase
Phase 3
Study type
Interventional
Enrollment
90 (actual)
Sponsor
Agios Pharmaceuticals, Inc. · Industry
Sex
All
Age
18 Years
Healthy volunteers
Not accepted

Summary

This is an open-label, multicenter, extension study to evaluate the long-term safety, tolerability, and efficacy of treatment with mitapivat in participants who were previously enrolled in Study AG348-C-006 or Study AG348-C-007.

Conditions

Interventions

TypeNameDescription
DRUGMitapivatTablets

Timeline

Start date
2019-03-21
Primary completion
2024-07-03
Completion
2024-07-03
First posted
2019-02-26
Last updated
2025-11-18
Results posted
2025-11-18

Locations

42 sites across 16 countries: United States, Brazil, Canada, Denmark, France, Germany, Ireland, Italy, Japan, Netherlands, South Korea, Spain, Switzerland, Thailand, Turkey (Türkiye), United Kingdom

Regulatory

Source: ClinicalTrials.gov record NCT03853798. Inclusion in this directory is not an endorsement.

Extension Study of AG-348 in Adult Participants With Pyruvate Kinase Deficiency Previously Enrolled in AG-348-006 or AG3 (NCT03853798) · Clinical Trials Directory