Trials / Completed
CompletedNCT03484767
"The MaP Study": Mapping the Patient Journey in MMA and PA
A Longitudinal, Exploratory, Natural History Study to Further Characterize and Describe the Signs and Symptoms of Patients With Organic Acidemias
- Status
- Completed
- Phase
- —
- Study type
- Observational
- Enrollment
- 97 (actual)
- Sponsor
- ModernaTX, Inc. · Industry
- Sex
- All
- Age
- —
- Healthy volunteers
- Not accepted
Summary
Longitudinal, exploratory, natural history study of patients with MMA due to mut deficiency and PA to characterize the changes in blood disease biomarkers over time and the frequency and severity of clinical events related to their disease.
Conditions
Timeline
- Start date
- 2018-03-20
- Primary completion
- 2021-05-29
- Completion
- 2021-05-29
- First posted
- 2018-04-02
- Last updated
- 2021-08-02
Locations
17 sites across 4 countries: United States, France, Spain, United Kingdom
Source: ClinicalTrials.gov record NCT03484767. Inclusion in this directory is not an endorsement.