Trials / Terminated
TerminatedNCT03347253
STRIDE Study - A Study in Subjects With LOPD Who Are Currently Being Treated With ERT
A Prospective Study in Subjects With Late Onset Pompe Disease Who Are Currently Being Treated With Enzyme Replacement Therapy
- Status
- Terminated
- Phase
- —
- Study type
- Observational
- Enrollment
- 12 (actual)
- Sponsor
- Amicus Therapeutics · Industry
- Sex
- All
- Age
- 18 Years – 75 Years
- Healthy volunteers
- Not accepted
Summary
The purpose of the study is to evaluate changes in key clinical outcome measures (eg, motor, respiratory, fatigue) in adult subjects with late-onset Pompe disease (LOPD) subjects receiving standard-of-care enzyme replacement therapy (ERT). Additionally, information gained may be used in the design and conduct of future studies in LOPD subjects.
Detailed description
The objective of this study is to evaluate the baseline characteristics and degree of change over time in clinical outcome measures commonly used to evaluate patients with LOPD.
Conditions
Timeline
- Start date
- 2017-12-08
- Primary completion
- 2018-11-30
- Completion
- 2018-11-30
- First posted
- 2017-11-20
- Last updated
- 2025-07-08
Locations
21 sites across 4 countries: United States, Australia, Belgium, Canada
Source: ClinicalTrials.gov record NCT03347253. Inclusion in this directory is not an endorsement.