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Trials / Approved For Marketing

Approved For MarketingNCT02963350

A Multicenter, Multi-national Open-label Program to Provide BMN 190 to Patients Diagnosed With CLN2 Disease

Status
Approved For Marketing
Phase
Study type
Expanded Access
Enrollment
Sponsor
BioMarin Pharmaceutical · Industry
Sex
All
Age
2 Years
Healthy volunteers

Summary

* To provide access to BMN 190 to patients with CLN2 disease who cannot participate in a clinical trial. * To collect additional information on the safety and tolerability of BMN 190 administration in patients with CLN2 disease.

Conditions

Interventions

TypeNameDescription
DRUGBMN190, recombinant human tripeptidyl peptidase-1 (rhTPP1)

Timeline

First posted
2016-11-15
Last updated
2017-07-24

Locations

5 sites across 4 countries: United States, Germany, Italy, United Kingdom

Source: ClinicalTrials.gov record NCT02963350. Inclusion in this directory is not an endorsement.

A Multicenter, Multi-national Open-label Program to Provide BMN 190 to Patients Diagnosed With CLN2 Disease (NCT02963350) · Clinical Trials Directory