Trials / Conditions / CLN2 Disease
CLN2 Disease
5 registered clinical trials studyying CLN2 Disease — 1 currently recruiting.
| Status | Trial | Sponsor | Phase |
|---|---|---|---|
| Recruiting | Natural History and Longitudinal Clinical Assessments in NCL / Batten Disease, the International DEM-CHILD Dat NCT04613089 | Universitätsklinikum Hamburg-Eppendorf | — |
| Completed | A Safety, Tolerability, and Efficacy Study of BMN 190 in Pediatric Patients < 18 Years of Age With CLN2 Diseas NCT02678689 | BioMarin Pharmaceutical | Phase 2 |
| Completed | An Extension Study to Evaluate the Long-Term Efficacy and Safety of BMN 190 in Patients With CLN2 Disease NCT02485899 | BioMarin Pharmaceutical | Phase 1 / Phase 2 |
| Completed | A Phase 1/2 Open-Label Dose-Escalation Study to Evaluate Safety, Tolerability, Pharmacokinetics, and Efficacy NCT01907087 | BioMarin Pharmaceutical | Phase 1 / Phase 2 |
| Approved For Marketing | A Multicenter, Multi-national Open-label Program to Provide BMN 190 to Patients Diagnosed With CLN2 Disease NCT02963350 | BioMarin Pharmaceutical | — |