Clinical Trials Directory

Trials / Terminated

TerminatedNCT02240355

A Study of RO6885247 in Adult and Pediatric Patients With Spinal Muscular Atrophy (MOONFISH)

A Multicenter, Randomized, Double Blind, Placebo Controlled, Multiple Dose Study to Investigate the Safety, Tolerability, Pharmacokinetics and Pharmacodynamics of RO6885247 Following 12 Weeks of Treatment in Adult and Pediatric Patients With Spinal Muscular Atrophy (MOONFISH).

Status
Terminated
Phase
Phase 1
Study type
Interventional
Enrollment
9 (actual)
Sponsor
Hoffmann-La Roche · Industry
Sex
All
Age
55 Years
Healthy volunteers
Not accepted

Summary

This multicenter, randomized, double-blind, 12-week, placebo-controlled multiple dose study will investigate the safety and tolerability of RO6885247 in adult and pediatric patients with spinal muscular atrophy (SMA).

Conditions

Interventions

TypeNameDescription
DRUGRO6885247oral solution
DRUGplacebooral solution

Timeline

Start date
2014-11-01
Primary completion
2015-07-01
Completion
2015-07-01
First posted
2014-09-15
Last updated
2016-12-22

Locations

26 sites across 9 countries: United States, Canada, France, Italy, Netherlands, Sweden, Switzerland, Turkey (Türkiye), United Kingdom

Source: ClinicalTrials.gov record NCT02240355. Inclusion in this directory is not an endorsement.