Trials / Terminated
TerminatedNCT02232477
Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in MPS I
An Extension Study of Intrathecal Enzyme Replacement for Cognitive Decline in Mucopolysaccharidosis I
- Status
- Terminated
- Phase
- N/A
- Study type
- Interventional
- Enrollment
- 6 (actual)
- Sponsor
- agnes chen · Academic / Other
- Sex
- All
- Age
- 6 Years
- Healthy volunteers
- Not accepted
Summary
This is a five-year extension study of the pilot study, "Intrathecal Enzyme Replacement for Cognitive Decline in MPS I". Participants must have completed the pilot study to participate in this study.
Conditions
Interventions
| Type | Name | Description |
|---|---|---|
| DRUG | Intrathecal recombinant human alpha iduronidase | Intrathecal recombinant human alpha iduronidase every 3 months |
Timeline
- Start date
- 2014-08-01
- Primary completion
- 2020-02-01
- Completion
- 2020-02-01
- First posted
- 2014-09-05
- Last updated
- 2023-10-31
- Results posted
- 2023-10-31
Locations
1 site across 1 country: United States
Source: ClinicalTrials.gov record NCT02232477. Inclusion in this directory is not an endorsement.