Clinical Trials Directory

Trials / Completed

CompletedNCT02176603

Observational Study of Endothelial Dysfunction in Phenylketonuria

Observational, Investigator Initiated, Monocentric Study of the Endothelial Dysfunction in Adolescent and Adult Patients With Phenylketonuria Due to Phenylalanine Hydroxylase Deficiency

Status
Completed
Phase
Study type
Observational
Enrollment
51 (actual)
Sponsor
Charite University, Berlin, Germany · Academic / Other
Sex
All
Age
16 Years
Healthy volunteers
Accepted

Summary

The purpose of this study is to determine whether adolescent and adult patients with phenylketonuria who are on long-term phenylalanine-restricted diet suffer from endothelial dysfunction.

Detailed description

The aim of the study is the examination of endothelial dysfunction and oxidative stress markers in adolescent and adult patients with phenylketonuria (PKU), in correlation to phenylalanine values und phenylalanine-restricted diet. 25-50 patients with PKU aged ≥16 years of age and a control group of 25 age- and sex-matched healthy volunteers will be included in the study. Endothelial dysfunction will be measured by venous occlusion plethysmography on the lower legs in the PKU patients and in the control group. Wave velocity, aortic stiffness, and intima media thickness of the common carotid artery will be measured by vicorder and duplex ultrasound scanner in the PKU patients and in the control group. Analyses of phenylalanine metabolites and renal function will be performed only in the PKU patients, analyses of oxidative stress markers in the PKU patients and in the control group. Dietary protocols of the patients with PKU will be calculated for their daily phenylalanine, total protein, and calorie intake. Results of the study will be kept in the medical records and paper case report forms. Data will be analyzed only in pseudonymized form.

Conditions

Timeline

Start date
2014-05-01
Primary completion
2015-07-22
Completion
2017-01-01
First posted
2014-06-27
Last updated
2017-02-23

Source: ClinicalTrials.gov record NCT02176603. Inclusion in this directory is not an endorsement.