Trials / Completed
CompletedNCT01920828
Gait Analysis in MPS IVA
Gait Analysis in Patients With MPS IVA Treated With Enzyme Replacement Therapy
- Status
- Completed
- Phase
- —
- Study type
- Observational
- Enrollment
- 10 (actual)
- Sponsor
- Oregon Health and Science University · Academic / Other
- Sex
- All
- Age
- 1 Year
- Healthy volunteers
- Not accepted
Summary
The purpose of this study is to learn about gait (walking) characteristics in MPS IVA and possible changes in gait with enzyme replacement therapy.
Detailed description
The purpose of this 3-year study is to conduct a longitudinal investigation using motion analysis of gait to objectively and quantitatively assess gait characteristics of MPS IVA patients. Data documenting gait characteristics and abnormalities will be gathered in patients initiating enzyme replacement therapy. Inclusion criteria Individuals with MPS IVA diagnosed by enzyme or molecular studies Exclusion Criteria Individual with MPS IVA previously enrolled in BMN-110 Individual is non-ambulatory The individual is unable to complete longitudinal study visits at least yearly
Conditions
Timeline
- Start date
- 2013-08-01
- Primary completion
- 2017-06-01
- Completion
- 2017-06-01
- First posted
- 2013-08-12
- Last updated
- 2019-10-17
Locations
1 site across 1 country: United States
Source: ClinicalTrials.gov record NCT01920828. Inclusion in this directory is not an endorsement.