Clinical Trials Directory

Trials / Conditions / MPS IVA

MPS IVA

12 registered clinical trials studyying MPS IVA — 3 currently recruiting.

StatusTrialSponsorPhase
RecruitingCardiac Structure and Function in MPS
NCT07361536
Children's Hospital of Orange County—
Active Not RecruitingSafety and Efficacy of Voxzogo for Growth Deficits in MPS IVA and VI
NCT05845749
University of California, San FranciscoPhase 1 / Phase 2
RecruitingPEARL (PrEnAtal Enzyme Replacement Therapy for Lysosomal Storage Disorders)
NCT04532047
University of California, San FranciscoPhase 1
RecruitingNon-invasive Functional Assessment and Pathogenesis of Morquio A
NCT05284006
Nemours Children's Clinic—
CompletedA Multicenter, Multinational, Observational Morquio A Registry Study (MARS)
NCT02294877
BioMarin Pharmaceutical—
CompletedScreening an Orthopedic Population for Mildly-affected Individuals With Morquio Syndrome A and Maroteaux-Lamy
NCT01961518
Greenwood Genetic Center—
CompletedGait Analysis in MPS IVA
NCT01920828
Oregon Health and Science University—
TerminatedEfficacy and Safety Study of BMN 110 for Morquio A Syndrome Patients Who Have Limited Ambulation
NCT01697319
BioMarin PharmaceuticalPhase 2
TerminatedSafety and Exercise Study of Two Doses of BMN 110 for Morquio A Syndrome
NCT01609062
BioMarin PharmaceuticalPhase 2
CompletedStudy of BMN 110 in Pediatric Patients < 5 Years of Age With Mucopolysaccharidosis IVA (Morquio A Syndrome)
NCT01515956
BioMarin PharmaceuticalPhase 2
CompletedLong-Term Efficacy and Safety Extension Study of BMN 110 in Patients With Mucopolysaccharidosis IVA (Morquio A
NCT01415427
BioMarin PharmaceuticalPhase 3
Approved For MarketingBMN 110 US Expanded Access Program
NCT01858103
BioMarin Pharmaceutical—